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Spinal Muscular Atrophy clinical trials in North Carolina
3 studies for Spinal Muscular Atrophy are looking for participants at sites in North Carolina.
Cities in North Carolina
A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- Rare Disease Research NC, LLC, Hillsborough
RecruitingPhase 2
Ages 5 to 17 · All sexes · Updated Sep 14, 2026 · NCT07287982Clinical Procedures to Support Research in ALS
- Duke University, Durham
- Wake Forest University, Winston-Salem
RecruitingObservational study
Ages 18 and older · All sexes · Updated Jun 15, 2026 · NCT03489278Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)
- Duke Health, Durham
RecruitingObservational study
All ages · All sexes · Updated Jan 31, 2025 · NCT04174157From ClinicalTrials.gov, data retrieved Oct 1, 2026. Each study sets its own eligibility; the study team decides who can join.