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Pag-aaral pangklinika para sa Spinal Muscular Atrophy sa California

11 pag-aaral para sa Spinal Muscular Atrophy ang naghahanap ng mga kalahok sa mga site sa California.

Mga Lungsod sa California

Opisyal na teksto ng pag-aaral (English)

A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy

  • Children's Hospital of Orange County (CHOC), Orange
  • Stanford Neuroscience Health Center (SNHC), Palo Alto
Nagre-recruitPhase 2
Hanggang edad 2 · Lahat ng kasarian · Na-update Okt 2, 2026 · NCT07047144

A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy

  • Stanford University Medical Center, Stanford
Nagre-recruitPhase 2
Edad 5 hanggang 17 · Lahat ng kasarian · Na-update Set 14, 2026 · NCT07287982

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy

  • Valley Children's Hospital, Madera
  • Stanford Univ Medical Center, Palo Alto
Nagre-recruitPhase 4
3 Months – 24 Months · Lahat ng kasarian · Na-update Set 10, 2026 · NCT05861999

A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)

  • Children's Hospital of Orange County, Orange
  • Stanford University Medical Center | Department of Neurology_Palo Alto, Palo Alto
Nagre-recruitPhase 1
Edad 3 pataas · Lahat ng kasarian · Na-update Set 3, 2026 · NCT06555419

Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy

  • Children's Hospital Orange County, Orange
  • Stanford Medical Center, Palo Alto
  • Rady Children's Hospital, San Diego
Nagre-recruit
Edad 3 pataas · Lahat ng kasarian · Na-update Ago 19, 2026 · NCT05866419

Clinical Procedures to Support Research in ALS

  • University of California, Irvine, Irvine
  • Stanford University, Palo Alto
  • California Pacific Medical Center, San Francisco
Nagre-recruitObservasyonal na pag-aaral
Edad 18 pataas · Lahat ng kasarian · Na-update Hun 15, 2026 · NCT03489278

ALS/MND Natural History Study Data Repository

  • Loma Linda University Health, Loma Linda
  • Kaiser Permanente, Los Angeles
Nagre-recruitObservasyonal na pag-aaral
Edad 18 hanggang 90 · Lahat ng kasarian · Na-update May 20, 2026 · NCT05966038

Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders

  • Stanford University, Palo Alto
Nagre-recruitObservasyonal na pag-aaralMalugod na tinatanggap ang malusog na boluntaryo
Edad 5 pataas · Lahat ng kasarian · Na-update Abr 9, 2026 · NCT06839469

A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their Babies

  • Stanford Neuroscience Health Center, Palo Alto
Nagre-recruitObservasyonal na pag-aaral
Edad 18 hanggang 54 · Kababaihan · Na-update Mar 9, 2026 · NCT05789758

Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)

  • Children's Hospital of Los Angeles, Los Angeles
  • University of California Los Angeles Health, Los Angeles
  • Valley Children's Healthcare, Madera
  • at 3 pa
Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update Ene 31, 2025 · NCT04174157

Mula sa ClinicalTrials.gov, na-kuha noong Okt 5, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.