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Pag-aaral pangklinika para sa Spinal Muscular Atrophy sa Texas

10 pag-aaral para sa Spinal Muscular Atrophy ang naghahanap ng mga kalahok sa mga site sa Texas.

Mga Lungsod sa Texas

Opisyal na teksto ng pag-aaral (English)

A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy

  • Neurology Rare Disease Center, Flower Mound
  • Texas Children's Hospital, Houston
Nagre-recruitPhase 2
Edad 5 hanggang 17 · Lahat ng kasarian · Na-update Set 14, 2026 · NCT07287982

A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy

  • University of Texas Southwestern Medical Center, Dallas
  • Neurology Rare Disease Center, Flower Mound
  • Cook Children's Medical Center, Fort Worth
  • at 1 pa
Nagre-recruitPhase 2
Hanggang edad 2 · Lahat ng kasarian · Na-update Set 14, 2026 · NCT07047144

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy

  • University of Texas Southwestern Medical Center, Dallas
Nagre-recruitPhase 4
3 Months – 24 Months · Lahat ng kasarian · Na-update Set 10, 2026 · NCT05861999

A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)

  • Texas Childrens Hospital Houston, Houston
Nagre-recruitPhase 1
Edad 3 pataas · Lahat ng kasarian · Na-update Set 3, 2026 · NCT06555419

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy

  • The University of Texas Southwestern Medical Center at Dallas, Dallas
  • Cook Children's Jane and John Justin Neurosciences Center, Fort Worth
Nagre-recruitPhase 4
3 Months – 24 Months · Lahat ng kasarian · Na-update Set 3, 2026 · NCT05861986

Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy

  • Texas Children's Hospital, Houston
Nagre-recruit
Edad 3 pataas · Lahat ng kasarian · Na-update Ago 19, 2026 · NCT05866419

A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety When Given Before Symptoms Appear in Babies With Genetically Diagnosed Spinal Muscular Atrophy (SMA)

  • Neurology Rare Disease Center, Flower Mound
Nagre-recruitPhase 3
0 Days – 42 Days · Lahat ng kasarian · Na-update Ago 18, 2026 · NCT07221669

A Study to Learn About the Safety and Effects of Salanersen (BIIB115) When Given to Babies With Spinal Muscular Atrophy (SMA) Who Were Previously Treated With Onasemnogene Abeparvovec

  • Neurology Rare Disease Center, Flower Mound
Nagre-recruitPhase 3
0 Days – 7 Months · Lahat ng kasarian · Na-update Ago 11, 2026 · NCT07444450

Clinical Procedures to Support Research in ALS

  • University of Texas San Antonio Health Science Center, San Antonio
Nagre-recruitObservasyonal na pag-aaral
Edad 18 pataas · Lahat ng kasarian · Na-update Hun 15, 2026 · NCT03489278

Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)

  • Cook Children's, Fort Worth
  • Texas Children's Hospital, Houston
  • CHRISTUS Health, San Antonio
Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update Ene 31, 2025 · NCT04174157

Mula sa ClinicalTrials.gov, na-kuha noong Okt 1, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.