Dachaigh › Dystrophy fèithe
Sgrùdaidhean clionaigeach Dystrophy fèithe a’ fastadh anns na SA
Tha 27 sgrùdaidhean airson Dystrophy fèithe a’ fastadh phàirtichean aig làraichean air feadh nan Stàitean Aonaichte.
Bailtean leis na sgrùdaidhean as motha
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Le stàit
- Arkansas3 sgrùdaidhean
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- North Carolina4 sgrùdaidhean
- Sgìre Cholumbia4 sgrùdaidhean
- Texas4 sgrùdaidhean
Sgrùdaidhean air an ùrachadh o chionn ghoirid
Teacsa sgrùdaidh oifigeil (Beurla)
Study of Inherited Neurological Disorders
A’ fastadhSgrùdadh amharc
Aoisean 2 gu 120 · Gach gnè · Air ùrachadh 28 Sult 2026 · NCT00004568Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy-SUMMIT
A’ fastadhSgrùdadh amharc
Aoisean 2 agus nas sine · Fir · Air ùrachadh 24 Sult 2026 · NCT06564974Investigational Use of Neuromuscular Ultrasound
A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Aoisean 18 gu 110 · Gach gnè · Air ùrachadh 17 Sult 2026 · NCT05237973Establishing Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1) Extension
A’ fastadhSgrùdadh amharc
Aoisean 18 gu 70 · Gach gnè · Air ùrachadh 4 Sult 2026 · NCT07700225Interfacing With NeuroTechnology to Expand Neural Throughput (INTENT)
A’ fastadh
Aoisean 18 gu 80 · Gach gnè · Air ùrachadh 2 Sult 2026 · NCT07521930Sodium/Glucose Cotransporter-2 Inhibitors (SGLT2i) Therapy in Duchenne Cardiomyopathy
A’ fastadhÌre 1
Aoisean 8 gu 18 · Fir · Air ùrachadh 24 Lùna 2026 · NCT07172971Evaluating VM100 Nutritional Supplement for Improving Quality of Life in Duchenne Muscular Dystrophy Patients
A’ fastadh
Aoisean 6 agus nas sine · Fir · Air ùrachadh 17 Lùna 2026 · NCT07766980Once Weekly Infant Corticosteroid Trial for DMD
A’ fastadhÌre 4
1 Month – 30 Months · Fir · Air ùrachadh 14 Lùna 2026 · NCT05412394Toward Ubiquitous Lower Limb Exoskeleton Use in Children and Young Adults
A’ fastadhSgrùdadh amharc
Aoisean 5 gu 25 · Gach gnè · Air ùrachadh 23 Iuch 2026 · NCT06998134A Study Evaluating the Real-World Experience of Givinostat in Patients With Duchenne Muscular Dystrophy
A’ fastadhSgrùdadh amharc
Aoisean 6 agus nas sine · Gach gnè · Air ùrachadh 2 Iuch 2026 · NCT07127978PBGENE-DMD Phase 1/2a Safety and Preliminary Efficacy Study in Duchenne Muscular Dystrophy (FUNCTION-DMD)
A’ fastadhÌre 1/2
Aoisean 2 gu 7 · Fir · Air ùrachadh 23 Ògmh 2026 · NCT07429240Feasibility of the BrainGate2 Neural Interface System in Persons With Tetraplegia
A’ fastadh
Aoisean 18 gu 80 · Gach gnè · Air ùrachadh 2 Ògmh 2026 · NCT05724173BrainGate2: Feasibility Study of an Intracortical Neural Interface System for Persons With Tetraplegia
A’ fastadh
Aoisean 18 gu 80 · Gach gnè · Air ùrachadh 1 Ògmh 2026 · NCT00912041Duchenne Electronic Health Record Study
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 27 Cèit 2026 · NCT07609394Efficacy, Safety, and Tolerability of Zeleciment Rostudirsen (DYNE-251) Administered Intravenously Every 4 Weeks in Ambulatory Participants With Duchenne Muscular Dystrophy (FORZETTO)
A’ fastadhÌre 3
Aoisean 4 gu 18 · Fir · Air ùrachadh 27 Cèit 2026 · NCT07608432Vasodilator and Exercise Study for DMD (VASO-REx)
A’ fastadhÌre 2
Aoisean 6 agus nas sine · Fir · Air ùrachadh 15 Cèit 2026 · NCT06290713Nomad P-KAFO Study
A’ fastadh
Aoisean 18 gu 89 · Gach gnè · Air ùrachadh 11 Cèit 2026 · NCT05644522The Duchenne Registry
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 8 Cèit 2026 · NCT02069756ECoG BMI for Motor and Speech Control
A’ fastadh
Aoisean 21 agus nas sine · Gach gnè · Air ùrachadh 5 Cèit 2026 · NCT03698149Muscle Health Measurements Using Electrical Impedance Myography
A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Aoisean 18 gu 89 · Gach gnè · Air ùrachadh 3 Gibl 2026 · NCT07502989Development of Quantitative Muscle Imaging as a Biomarker of Disease Endpoints in Myotonic Dystrophy
A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Aoisean 18 gu 65 · Gach gnè · Air ùrachadh 23 Faoi 2026 · NCT07362875Feasibility of the BrainGate2 Neural Interface System in Persons With Tetraplegia (BG-Speech-02)
A’ fastadh
Aoisean 18 gu 80 · Gach gnè · Air ùrachadh 1 Dùbh 2025 · NCT06094205Long-Term Development of Muscular Dystrophy Outcome Assessments
A’ fastadhSgrùdadh amharc
Aoisean 6 gu 50 · Gach gnè · Air ùrachadh 18 Samh 2025 · NCT05989620Evaluating Long-term Use of a Pediatric Robotic Exoskeleton (P.REX/Agilik) to Improve Gait in Children With Movement Disorders
A’ fastadh
Aoisean 3 gu 17 · Gach gnè · Air ùrachadh 27 Dàmh 2025 · NCT05726591Myotonic Dystrophy and Facioscapulohumeral Muscular Dystrophy Registry
A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Gach aois · Gach gnè · Air ùrachadh 15 Dàmh 2025 · NCT00082108Bho ClinicalTrials.gov, dàta air a thogail 5 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.