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Sgrùdaidhean clionaigeach Dystrophy fèithe a’ fastadh anns na SA

Tha 27 sgrùdaidhean airson Dystrophy fèithe a’ fastadh phàirtichean aig làraichean air feadh nan Stàitean Aonaichte.

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Teacsa sgrùdaidh oifigeil (Beurla)

Study of Inherited Neurological Disorders

A’ fastadhSgrùdadh amharc
Aoisean 2 gu 120 · Gach gnè · Air ùrachadh 28 Sult 2026 · NCT00004568

Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy-SUMMIT

A’ fastadhSgrùdadh amharc
Aoisean 2 agus nas sine · Fir · Air ùrachadh 24 Sult 2026 · NCT06564974

Investigational Use of Neuromuscular Ultrasound

A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Aoisean 18 gu 110 · Gach gnè · Air ùrachadh 17 Sult 2026 · NCT05237973

Establishing Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1) Extension

A’ fastadhSgrùdadh amharc
Aoisean 18 gu 70 · Gach gnè · Air ùrachadh 4 Sult 2026 · NCT07700225

Interfacing With NeuroTechnology to Expand Neural Throughput (INTENT)

A’ fastadh
Aoisean 18 gu 80 · Gach gnè · Air ùrachadh 2 Sult 2026 · NCT07521930

Sodium/Glucose Cotransporter-2 Inhibitors (SGLT2i) Therapy in Duchenne Cardiomyopathy

A’ fastadhÌre 1
Aoisean 8 gu 18 · Fir · Air ùrachadh 24 Lùna 2026 · NCT07172971

Evaluating VM100 Nutritional Supplement for Improving Quality of Life in Duchenne Muscular Dystrophy Patients

A’ fastadh
Aoisean 6 agus nas sine · Fir · Air ùrachadh 17 Lùna 2026 · NCT07766980

Once Weekly Infant Corticosteroid Trial for DMD

A’ fastadhÌre 4
1 Month – 30 Months · Fir · Air ùrachadh 14 Lùna 2026 · NCT05412394

Toward Ubiquitous Lower Limb Exoskeleton Use in Children and Young Adults

A’ fastadhSgrùdadh amharc
Aoisean 5 gu 25 · Gach gnè · Air ùrachadh 23 Iuch 2026 · NCT06998134

A Study Evaluating the Real-World Experience of Givinostat in Patients With Duchenne Muscular Dystrophy

A’ fastadhSgrùdadh amharc
Aoisean 6 agus nas sine · Gach gnè · Air ùrachadh 2 Iuch 2026 · NCT07127978

PBGENE-DMD Phase 1/2a Safety and Preliminary Efficacy Study in Duchenne Muscular Dystrophy (FUNCTION-DMD)

A’ fastadhÌre 1/2
Aoisean 2 gu 7 · Fir · Air ùrachadh 23 Ògmh 2026 · NCT07429240

Feasibility of the BrainGate2 Neural Interface System in Persons With Tetraplegia

A’ fastadh
Aoisean 18 gu 80 · Gach gnè · Air ùrachadh 2 Ògmh 2026 · NCT05724173

BrainGate2: Feasibility Study of an Intracortical Neural Interface System for Persons With Tetraplegia

A’ fastadh
Aoisean 18 gu 80 · Gach gnè · Air ùrachadh 1 Ògmh 2026 · NCT00912041

Duchenne Electronic Health Record Study

A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 27 Cèit 2026 · NCT07609394

Vasodilator and Exercise Study for DMD (VASO-REx)

A’ fastadhÌre 2
Aoisean 6 agus nas sine · Fir · Air ùrachadh 15 Cèit 2026 · NCT06290713

Nomad P-KAFO Study

A’ fastadh
Aoisean 18 gu 89 · Gach gnè · Air ùrachadh 11 Cèit 2026 · NCT05644522

The Duchenne Registry

A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 8 Cèit 2026 · NCT02069756

ECoG BMI for Motor and Speech Control

A’ fastadh
Aoisean 21 agus nas sine · Gach gnè · Air ùrachadh 5 Cèit 2026 · NCT03698149

Muscle Health Measurements Using Electrical Impedance Myography

A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Aoisean 18 gu 89 · Gach gnè · Air ùrachadh 3 Gibl 2026 · NCT07502989

Development of Quantitative Muscle Imaging as a Biomarker of Disease Endpoints in Myotonic Dystrophy

A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Aoisean 18 gu 65 · Gach gnè · Air ùrachadh 23 Faoi 2026 · NCT07362875

Feasibility of the BrainGate2 Neural Interface System in Persons With Tetraplegia (BG-Speech-02)

A’ fastadh
Aoisean 18 gu 80 · Gach gnè · Air ùrachadh 1 Dùbh 2025 · NCT06094205

Long-Term Development of Muscular Dystrophy Outcome Assessments

A’ fastadhSgrùdadh amharc
Aoisean 6 gu 50 · Gach gnè · Air ùrachadh 18 Samh 2025 · NCT05989620

Evaluating Long-term Use of a Pediatric Robotic Exoskeleton (P.REX/Agilik) to Improve Gait in Children With Movement Disorders

A’ fastadh
Aoisean 3 gu 17 · Gach gnè · Air ùrachadh 27 Dàmh 2025 · NCT05726591

Myotonic Dystrophy and Facioscapulohumeral Muscular Dystrophy Registry

A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Gach aois · Gach gnè · Air ùrachadh 15 Dàmh 2025 · NCT00082108

Bho ClinicalTrials.gov, dàta air a thogail 5 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.