Akèy › Twoub Sikl Urè Konjenital
Etid klinik pou Twoub Sikl Urè Konjenital ap rekrite nan Etazini
7 etid pou Twoub Sikl Urè Konjenital ap rekrite patisipan nan sit atravè Etazini.
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Long-term Follow-up (LTFU) Study of Participants in Any iECURE Protocol Using an Investigational Product (IP)
Ap rekriteEtid obsèvasyon
7 Months – 15 Months · Tout sèks · Mizajou Aug 31, 2026 · NCT06805695Study of LNP.UCD.ABE in Patients With Urea Cycle Disorders
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24 Hours – 5 Years · Tout sèks · Mizajou Aug 26, 2026 · NCT07667387Functional Evaluation in Patients With Urea Cycle Disorders (UCD) During a Driving Task
Ap rekriteEtid obsèvasyonVolontè an sante akeyi
Laj 16 a 40 · Tout sèks · Mizajou Jul 31, 2026 · NCT07701694At Home Ammonia Monitoring of Inborn Errors of Ammonia Metabolism
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Laj 12 ak plis · Tout sèks · Mizajou May 27, 2026 · NCT06953505Hepatic Histopathology in Urea Cycle Disorders
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Tout laj · Tout sèks · Mizajou Jul 20, 2025 · NCT04908319Systemic Biomarkers of Brain Injury From Hyperammonemia
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Laj 7 a 18 · Tout sèks · Mizajou Feb 7, 2024 · NCT04602325Orphan Europe Carbaglu® Surveillance Protocol
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Tout laj · Tout sèks · Mizajou Feb 7, 2024 · NCT03409003Sous ClinicalTrials.gov, done yo ranmase Oct 2, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.