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Tèks ofisyèl etid la (Anglè)

Long-term Follow-up (LTFU) Study of Participants in Any iECURE Protocol Using an Investigational Product (IP)

Ap rekriteEtid obsèvasyon
7 Months – 15 Months · Tout sèks · Mizajou Aug 31, 2026 · NCT06805695

Study of LNP.UCD.ABE in Patients With Urea Cycle Disorders

Ap rekriteFaz 1/2
24 Hours – 5 Years · Tout sèks · Mizajou Aug 26, 2026 · NCT07667387

Functional Evaluation in Patients With Urea Cycle Disorders (UCD) During a Driving Task

Ap rekriteEtid obsèvasyonVolontè an sante akeyi
Laj 16 a 40 · Tout sèks · Mizajou Jul 31, 2026 · NCT07701694

At Home Ammonia Monitoring of Inborn Errors of Ammonia Metabolism

Ap rekrite
Laj 12 ak plis · Tout sèks · Mizajou May 27, 2026 · NCT06953505

Hepatic Histopathology in Urea Cycle Disorders

Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Jul 20, 2025 · NCT04908319

Systemic Biomarkers of Brain Injury From Hyperammonemia

Ap rekriteEtid obsèvasyon
Laj 7 a 18 · Tout sèks · Mizajou Feb 7, 2024 · NCT04602325

Orphan Europe Carbaglu® Surveillance Protocol

Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Feb 7, 2024 · NCT03409003

Sous ClinicalTrials.gov, done yo ranmase Oct 2, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.