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A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
- Columbia University Medical Center, New York
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3 Months – 24 Months · Tout sèks · Mizajou Oct 2, 2026 · NCT05861986ASsessing The REAl-world Safety & Effectiveness of Spinal Muscular Atrophy Participants Treated With Intrathecal Onasemnogene Abeparvovec-brve (OAV101B) (ITVISMA®): A U.S. Pragmatic Multicenter Study (STREAM)
- Columbia University Medical Center, New York
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Laj 2 a 100 · Tout sèks · Mizajou Sep 18, 2026 · NCT07448610A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- Columbia University Herbert Irving Comprehensive Cancer Center, New York
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Laj 5 a 17 · Tout sèks · Mizajou Sep 14, 2026 · NCT07287982Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy
- Columbia University Irving Medical Center/NewYork Presbyterian Hospital, New York
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Laj 3 ak plis · Tout sèks · Mizajou Aug 19, 2026 · NCT05866419Characterizing Perceived Physical Fatigability in Nusinersen-treated SMA
- Columbia University Irving Medical Center, New York
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Laj 12 ak plis · Tout sèks · Mizajou May 14, 2026 · NCT06955897Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders
- Columbia University Irving Medical Center, New York
Ap rekriteEtid obsèvasyonVolontè an sante akeyi
Laj 5 ak plis · Tout sèks · Mizajou Apr 9, 2026 · NCT06839469HABIT-ILE + FST in Children With SMA: Preliminary Effectiveness
- Center for Cerebral Palsy Research, Teachers College, Columbia University, New York
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Laj 5 a 17 · Tout sèks · Mizajou Mar 23, 2026 · NCT07488338Gait and Bone Health in SMA
- Columbia University Irving Medical Center, New York
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Laj 8 a 50 · Tout sèks · Mizajou Mar 18, 2026 · NCT07400198A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their Babies
- Columbia University Irving Medical Center, New York
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Laj 18 a 54 · Fanm · Mizajou Mar 9, 2026 · NCT05789758Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)
- University of Rochester Medical Center, Rochester
- The State University of New York, Stony Brook
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Tout laj · Tout sèks · Mizajou Jan 31, 2025 · NCT04174157Sous ClinicalTrials.gov, done yo ranmase Oct 5, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.