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Beranda › Atrofi Otot Tulang Belakang › New York › New York City

Uji klinis Atrofi Otot Tulang Belakang di New York City, NY

9 studi untuk Atrofi Otot Tulang Belakang mencari peserta di lokasi sekitar New York City (dalam radius sekitar 30 mil). Buka studi untuk melihat kriteria peserta dan cara menghubungi tim studi.

Teks studi resmi (Bahasa Inggris)

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A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy

Menerima pesertaFase 4
  • Columbia University Medical Center, New York
3 Months – 24 Months · Semua jenis kelamin · Diperbarui 2 Okt 2026 · NCT05861986

ASsessing The REAl-world Safety & Effectiveness of Spinal Muscular Atrophy Participants Treated With Intrathecal Onasemnogene Abeparvovec-brve (OAV101B) (ITVISMA®): A U.S. Pragmatic Multicenter Study (STREAM)

Menerima pesertaFase 4
  • Columbia University Medical Center, New York
Usia 2 hingga 100 · Semua jenis kelamin · Diperbarui 18 Sep 2026 · NCT07448610

A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy

Menerima pesertaFase 2
  • Columbia University Herbert Irving Comprehensive Cancer Center, New York
Usia 5 hingga 17 · Semua jenis kelamin · Diperbarui 14 Sep 2026 · NCT07287982

Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy

Menerima peserta
  • Columbia University Irving Medical Center/NewYork Presbyterian Hospital, New York
Usia 3 ke atas · Semua jenis kelamin · Diperbarui 19 Agu 2026 · NCT05866419

Characterizing Perceived Physical Fatigability in Nusinersen-treated SMA

Menerima pesertaStudi observasional
  • Columbia University Irving Medical Center, New York
Usia 12 ke atas · Semua jenis kelamin · Diperbarui 14 Mei 2026 · NCT06955897

Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders

Menerima pesertaStudi observasionalSukarelawan sehat diterima
  • Columbia University Irving Medical Center, New York
Usia 5 ke atas · Semua jenis kelamin · Diperbarui 9 Apr 2026 · NCT06839469

HABIT-ILE + FST in Children With SMA: Preliminary Effectiveness

Menerima peserta
  • Center for Cerebral Palsy Research, Teachers College, Columbia University, New York
Usia 5 hingga 17 · Semua jenis kelamin · Diperbarui 23 Mar 2026 · NCT07488338

Gait and Bone Health in SMA

Menerima pesertaStudi observasional
  • Columbia University Irving Medical Center, New York
Usia 8 hingga 50 · Semua jenis kelamin · Diperbarui 18 Mar 2026 · NCT07400198

A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their Babies

Menerima pesertaStudi observasional
  • Columbia University Irving Medical Center, New York
Usia 18 hingga 54 · Wanita · Diperbarui 9 Mar 2026 · NCT05789758

Uji klinis Atrofi Otot Tulang Belakang di kota lain

Studi lain di New York City

Dari ClinicalTrials.gov, data diambil 6 Okt 2026. Setiap studi menetapkan kriteria kelayakannya sendiri; tim studi yang menentukan siapa yang bisa bergabung.