ニューヨークにおける脊髄性筋萎縮症の臨床試験
ニューヨーク内の拠点で、脊髄性筋萎縮症に関する10件の研究が参加者を募集しています。
ニューヨーク内の都市
公式研究テキスト（英語）
A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
- Columbia University Medical Center, New York
被験者募集中第4相
3 Months – 24 Months · 全性別 · 2026/10/02更新 · NCT05861986ASsessing The REAl-world Safety & Effectiveness of Spinal Muscular Atrophy Participants Treated With Intrathecal Onasemnogene Abeparvovec-brve (OAV101B) (ITVISMA®): A U.S. Pragmatic Multicenter Study (STREAM)
- Columbia University Medical Center, New York
被験者募集中第4相
2歳〜100歳 · 全性別 · 2026/09/18更新 · NCT07448610A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- Columbia University Herbert Irving Comprehensive Cancer Center, New York
被験者募集中第2相
5歳〜17歳 · 全性別 · 2026/09/14更新 · NCT07287982Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy
- Columbia University Irving Medical Center/NewYork Presbyterian Hospital, New York
被験者募集中
3歳以上 · 全性別 · 2026/08/19更新 · NCT05866419Characterizing Perceived Physical Fatigability in Nusinersen-treated SMA
- Columbia University Irving Medical Center, New York
被験者募集中観察研究
12歳以上 · 全性別 · 2026/05/14更新 · NCT06955897Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders
- Columbia University Irving Medical Center, New York
被験者募集中観察研究健康なボランティア歓迎
5歳以上 · 全性別 · 2026/04/09更新 · NCT06839469HABIT-ILE + FST in Children With SMA: Preliminary Effectiveness
- Center for Cerebral Palsy Research, Teachers College, Columbia University, New York
被験者募集中
5歳〜17歳 · 全性別 · 2026/03/23更新 · NCT07488338Gait and Bone Health in SMA
- Columbia University Irving Medical Center, New York
被験者募集中観察研究
8歳〜50歳 · 全性別 · 2026/03/18更新 · NCT07400198A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their Babies
- Columbia University Irving Medical Center, New York
被験者募集中観察研究
18歳〜54歳 · 女性 · 2026/03/09更新 · NCT05789758Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)
- University of Rochester Medical Center, Rochester
- The State University of New York, Stony Brook
被験者募集中観察研究
全年齢 · 全性別 · 2025/01/31更新 · NCT04174157ClinicalTrials.govより、2026/10/05時点のデータを取得。各研究には独自の参加資格があり、参加可否は研究チームが決定します。