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Retos ligos klinikiniai tyrimai Kalifornija

10 tyrimai dėl Retos ligos ieško dalyvių vietose Kalifornija.

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Oficialus tyrimo tekstas (anglų kalba)

Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network

  • University of California, Los Angeles, Los Angeles
  • University of California, Irvine Medical Center, Orange
  • Stanford University, Stanford
  • ir dar 2
Renkami dalyviaiStebimasis tyrimasLaukiami sveiki savanoriai
1 Month – 100 Years · Visoms lytims · Atnaujinta 2026-10-02 · NCT02450851

A Study of SGT-212 Gene Therapy in Friedreich's Ataxia

  • The University of California, Los Angeles (UCLA), Los Angeles
Renkami dalyviai1 fazė
Amžius nuo 18 iki 40 · Visoms lytims · Atnaujinta 2026-09-29 · NCT07180355

A First-in-human Study of KK8123 in Adults With X-linked Hypophosphatemia

  • University of California - San Francisco, San Francisco
Renkami dalyviai1/2 fazė
Amžius nuo 18 iki 65 · Visoms lytims · Atnaujinta 2026-09-21 · NCT06525636

Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study

  • UCLA Ataxia Center, Los Angeles
Renkami dalyviaiStebimasis tyrimasLaukiami sveiki savanoriai
Visi amžiai · Visoms lytims · Atnaujinta 2026-09-01 · NCT06016946

International Rare Brain Tumor Registry

  • Children's Hospital Los Angeles, Los Angeles
  • University of California San Francisco, San Francisco
Renkami dalyviaiStebimasis tyrimas
Iki 45 metų · Visoms lytims · Atnaujinta 2026-08-07 · NCT05697874

Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

  • University of California - Irvine Medical Center, Irvine
Renkami dalyviai2 fazė
Amžius 18 ir vyresni · Visoms lytims · Atnaujinta 2026-06-23 · NCT07123155

A Study of AAV9 Gene Therapy in Participants With Canavan Disease (CANaspire Clinical Trial)

  • UCSF Benioff Children's Hospital Oakland, Oakland
Renkami dalyviai1/2 fazė
30 Months · Visoms lytims · Atnaujinta 2026-04-17 · NCT04998396

The ExTINGUISH Trial of Inebilizumab in NMDAR Encephalitis

  • Children's Hospital of Orange County, Orange
  • UC Irvine, Orange
  • UC Davis, Sacramento
Renkami dalyviai2 fazė
Amžius 12 ir vyresni · Visoms lytims · Atnaujinta 2025-07-01 · NCT04372615

Prospective Observational International Registry of Patients With Newly Diagnosed Peripheral T Cell Lymphoma.

  • Stanford University, Stanford
Renkami dalyviaiStebimasis tyrimas
Amžius 18 ir vyresni · Visoms lytims · Atnaujinta 2025-05-06 · NCT03964480

Epilepsy Learning Healthcare System (ELHS)

  • Children's Hospital Los Angeles, Los Angeles
  • University of Southern California, Los Angeles
Renkami dalyviaiStebimasis tyrimas
Visi amžiai · Visoms lytims · Atnaujinta 2024-08-30 · NCT06265103

Iš ClinicalTrials.gov, duomenys gauti 2026-10-05. Kiekvienas tyrimas nustato savo tinkamumo kriterijus; tyrimo komanda sprendžia, kas gali dalyvauti.