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Rare Diseases clinical trials in Los Angeles, CA
5 studies for Rare Diseases are looking for participants at sites in and around Los Angeles (within about 30 miles). Open a study to see who can join and how to contact the study team.
Recruiting for a study here? Feature it at the top of this page — $99 for 30 days →
Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network
RecruitingObservational studyHealthy volunteers welcome
- University of California, Los Angeles, Los Angeles
A Study of SGT-212 Gene Therapy in Friedreich's Ataxia
RecruitingPhase 1
- The University of California, Los Angeles (UCLA), Los Angeles
Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study
RecruitingObservational studyHealthy volunteers welcome
- UCLA Ataxia Center, Los Angeles
International Rare Brain Tumor Registry
RecruitingObservational study
- Children's Hospital Los Angeles, Los Angeles
Epilepsy Learning Healthcare System (ELHS)
RecruitingObservational study
- Children's Hospital Los Angeles, Los Angeles
- University of Southern California, Los Angeles
About Rare Diseases
A rare disease is one that affects fewer than 200,000 people in the United States. There are nearly 7,000, affecting more than 25 million Americans.
More about Rare Diseases on MedlinePlus
Rare Diseases trials in other cities
- Boston, MA9 studies
- Washington, DC8 studies
- Chicago, IL8 studies
- Philadelphia, PA7 studies
- Cincinnati, OH5 studies
- Columbus, OH4 studies
- New York City, NY3 studies
- Houston, TX3 studies
- Nashville, TN3 studies
- Seattle, WA3 studies
- Rochester, MN3 studies
- St. Louis, MO3 studies
Other studies in Los Angeles
- Non-Small Cell Lung Cancer87 studies
- Cancer (all types)74 studies
- Breast Cancer73 studies
- Prostate Cancer61 studies
- Colorectal Cancer59 studies
- Metastatic Cancer57 studies
- Ovarian Cancer50 studies
- Lung Cancer45 studies
- Head and Neck Squamous Cell Carcinoma42 studies
- Pancreatic Cancer35 studies
- Endometrial Cancer34 studies
- Melanoma34 studies
From ClinicalTrials.gov, data retrieved Oct 6, 2026. Each study sets its own eligibility; the study team decides who can join.