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Spinal Muscular Atrophy clinical trials in California
11 studies for Spinal Muscular Atrophy are looking for participants at sites in California.
Cities in California
A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy
- Children's Hospital of Orange County (CHOC), Orange
- Stanford Neuroscience Health Center (SNHC), Palo Alto
RecruitingPhase 2
Up to age 2 · All sexes · Updated Oct 2, 2026 · NCT07047144A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety in Participants Aged 15 to 60 Years With Spinal Muscular Atrophy (SMA) Who Are Either New to SMA Treatment or Were Previously Treated With Risdiplam
- Stanford University Medical Center, Palo Alto
RecruitingPhase 3
Ages 15 to 60 · All sexes · Updated Oct 2, 2026 · NCT07444476A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- Stanford University Medical Center, Stanford
RecruitingPhase 2
Ages 5 to 17 · All sexes · Updated Sep 14, 2026 · NCT07287982A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy
- Valley Children's Hospital, Madera
- Stanford Univ Medical Center, Palo Alto
RecruitingPhase 4
3 Months – 24 Months · All sexes · Updated Sep 10, 2026 · NCT05861999A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)
- Children's Hospital of Orange County, Orange
- Stanford University Medical Center | Department of Neurology_Palo Alto, Palo Alto
RecruitingPhase 1
Ages 3 and older · All sexes · Updated Sep 3, 2026 · NCT06555419Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy
- Children's Hospital Orange County, Orange
- Stanford Medical Center, Palo Alto
- Rady Children's Hospital, San Diego
Recruiting
Ages 3 and older · All sexes · Updated Aug 19, 2026 · NCT05866419Clinical Procedures to Support Research in ALS
- University of California, Irvine, Irvine
- Stanford University, Palo Alto
- California Pacific Medical Center, San Francisco
RecruitingObservational study
Ages 18 and older · All sexes · Updated Jun 15, 2026 · NCT03489278ALS/MND Natural History Study Data Repository
- Loma Linda University Health, Loma Linda
- Kaiser Permanente, Los Angeles
RecruitingObservational study
Ages 18 to 90 · All sexes · Updated May 20, 2026 · NCT05966038Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders
- Stanford University, Palo Alto
RecruitingObservational studyHealthy volunteers welcome
Ages 5 and older · All sexes · Updated Apr 9, 2026 · NCT06839469A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their Babies
- Stanford Neuroscience Health Center, Palo Alto
RecruitingObservational study
Ages 18 to 54 · Women · Updated Mar 9, 2026 · NCT05789758Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)
- Children's Hospital of Los Angeles, Los Angeles
- University of California Los Angeles Health, Los Angeles
- Valley Children's Healthcare, Madera
- and 3 more
RecruitingObservational study
All ages · All sexes · Updated Jan 31, 2025 · NCT04174157From ClinicalTrials.gov, data retrieved Oct 5, 2026. Each study sets its own eligibility; the study team decides who can join.