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Gaucher Disease clinical trials in San Francisco, CA
4 studies for Gaucher Disease are looking for participants at sites in and around San Francisco (within about 30 miles). Open a study to see who can join and how to contact the study team.
Recruiting for a study here? Feature it at the top of this page — $99 for 30 days →
A Gaucher Disease Gene Therapy Trial With FLT201
RecruitingPhase 3
- University of California, San Francisco (UCSF), San Francisco
International Collaborative Gaucher Group (ICGG) Gaucher Disease Registry & Pregnancy Sub-registry
RecruitingObservational study
- University of California San Francisco - Parnassus Campus- Site Number : 840051, San Francisco
Registry of Patients Diagnosed With Lysosomal Storage Diseases
RecruitingObservational study
- University of California San Francisco, San Francisco
PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)
RecruitingPhase 1
- University of California, San Francisco
About Gaucher Disease
Gaucher disease is a rare, inherited disorder in which you do not have enough of an enzyme called glucocerebrosidase. Learn about the three types.
More about Gaucher Disease on MedlinePlus
Gaucher Disease trials in other cities
Other studies in San Francisco
- Prostate Cancer45 studies
- Breast Cancer43 studies
- Non-Small Cell Lung Cancer36 studies
- Cancer (all types)35 studies
- Heart Failure29 studies
- Metastatic Cancer28 studies
- Lung Cancer22 studies
- Melanoma22 studies
- Pancreatic Cancer20 studies
- Ovarian Cancer19 studies
- Colorectal Cancer18 studies
- Cardiovascular Disease18 studies
From ClinicalTrials.gov, data retrieved Oct 6, 2026. Each study sets its own eligibility; the study team decides who can join.