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Kajian klinikal Penyakit Sel Sabit di Pennsylvania

20 kajian untuk Penyakit Sel Sabit sedang mencari peserta di lokasi di Pennsylvania.

Bandar di Pennsylvania

Teks kajian rasmi (Bahasa Inggeris)

A Study to Investigate the Efficacy and Safety of Crizanlizumab (5 mg/kg) Compared With Placebo in Adolescent and Adult Sickle Cell Disease Patients Who Experience Frequent Vaso-Occlusive Crises (SPARKLE)

  • Spoknwrdclinicaltrials, Easton
  • Thomas Jefferson University Me, Philadelphia
Mengambil pesertaFasa 3
Umur 12 hingga 100 · Semua jantina · Dikemas kini 28 Sep 2026 · NCT06439082

A Phase 1b, Open-Label Study of DISC-3405 in Participants With Sickle Cell Disease (SCD)

  • University of Pittsburgh Medical Center (UPMC), Pittsburgh
Mengambil pesertaFasa 1
Umur 18 ke atas · Semua jantina · Dikemas kini 23 Sep 2026 · NCT07187973

A Study to Evaluate How Well Etavopivat Works in People With Sickle Cell Disease

  • Children's Hosptl Philadelphia, Philadelphia
  • St Christopher Hosp for Child, Philadelphia
Mengambil pesertaFasa 3
Umur 12 ke atas · Semua jantina · Dikemas kini 17 Sep 2026 · NCT06612268

A Phase I/II Study of ITU512 in Healthy Participants and Patients With Sickle Cell Disease

  • Childrens Hospital Of Philadelphia, Philadelphia
Mengambil pesertaFasa 1/2Sukarelawan sihat dialu-alukan
Umur 12 hingga 55 · Semua jantina · Dikemas kini 9 Sep 2026 · NCT06546670

A Study to Evaluate BMS-986470 in Healthy Volunteers and Participants With Sickle Cell Disease

  • Local Institution - 0029, Philadelphia
  • Thomas Jefferson University - Medicine/GI and Hepatology, Philadelphia
  • Local Institution - 0032, Pittsburgh
Mengambil pesertaFasa 1/2Sukarelawan sihat dialu-alukan
Umur 18 ke atas · Semua jantina · Dikemas kini 18 Ogo 2026 · NCT06481306

ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders

  • Children's Hospital of Philadelphia, Philadelphia
  • Penn Comprehensive Hemophilia and Thrombophilia Program/Hospital of the University of Pennsylvania, Philadelphia
  • St. Christopher's Hospital for Children, Philadelphia
  • dan 1 lagi
Mengambil pesertaKajian pemerhatian
Semua umur · Semua jantina · Dikemas kini 17 Ogo 2026 · NCT04398628

Safety, Efficacy, and Pharmacokinetics of CSL889 in Adults and Adolescents With Sickle Cell Disease During Vaso-Occlusive Crisis

  • University of Pittsburgh, Pittsburgh
  • Hillman Cancer Center, Pittsburgh
Mengambil pesertaFasa 2
Umur 12 ke atas · Semua jantina · Dikemas kini 14 Ogo 2026 · NCT06699849

T-Cell Depleted Alternative Donor Bone Marrow Transplant for Sickle Cell Disease (SCD) and Other Anemias

  • Children's Hospital of Pittsburgh of UPMC, Pittsburgh
Mengambil pesertaFasa 1/2
Umur 5 hingga 40 · Semua jantina · Dikemas kini 13 Ogo 2026 · NCT03653338

Ruxolitinib-Enhanced Haplo HCT for Children and Young Adults With Sickle Cell Disease

  • Children's Hospital of Philadelphia, Philadelphia
Mengambil pesertaFasa 1/2
Umur 12 hingga 45 · Semua jantina · Dikemas kini 4 Jun 2026 · NCT07252050

Comparing the Effectiveness of Matched Related Donor Hematopoietic Stem Cell Transplantation to Disease Modifying Therapy in Pediatric Patients With Sickle Cell Disease

  • Children's Hospital of Philadelphia (MRD-HCT), Philadelphia
Mengambil pesertaKajian pemerhatian
Umur 3 hingga 20 · Semua jantina · Dikemas kini 4 Jun 2026 · NCT06941389

Clinical and Biomarker Effects of Depot Medroxyprogesterone Acetate in Females With Sickle Cell Disease

  • Children's Hospital of Philadelphia, Philadelphia
Mengambil pesertaFasa 4
Umur 18 hingga 50 · Wanita · Dikemas kini 28 Mei 2026 · NCT06665997

A Socio-ecological Approach for Improving Self-management in Adolescents With SCD

  • Children's Hospital of Philadelphia, Philadelphia
Mengambil peserta
Umur 13 hingga 21 · Semua jantina · Dikemas kini 11 Mei 2026 · NCT06290401

Zinc Supplementation in Sickle Cell Disease: A Precursor to the Think Zinc for Bones Trial

  • Children's Hospital of Philadelphia, Philadelphia
  • Thomas Jefferson University Hospital, Philadelphia
Mengambil pesertaFasa 2
Umur 15 hingga 40 · Semua jantina · Dikemas kini 13 Mac 2026 · NCT06260891

Stress Management and Mindfulness Intervention for Patients With Sickle Cell Disease

  • University of Pennsylvania, Philadelphia
Mengambil peserta
Umur 18 ke atas · Semua jantina · Dikemas kini 27 Feb 2026 · NCT07316478

A Long-term Follow-up Study in Patients Who Received BEAM-101

  • Children's Hospital of Philadelphia, Philadelphia
Mengambil pesertaKajian pemerhatian
Umur 14 hingga 37 · Semua jantina · Dikemas kini 28 Jan 2026 · NCT07373639

Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
Mengambil pesertaKajian pemerhatian
2 Months – 60 Years · Semua jantina · Dikemas kini 13 Jan 2026 · NCT04528355

Peer Support for Adolescents and Emerging Adults With Sickle Cell Pain

  • UPMC University of Pittsburgh Classical Hematology Adult Clinic, Pittsburgh
  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
Mengambil peserta
Umur 16 hingga 30 · Semua jantina · Dikemas kini 7 Jan 2026 · NCT06374238

Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
Mengambil pesertaFasa 2
2 Months – 55 Years · Semua jantina · Dikemas kini 15 Dis 2025 · NCT01962415

Cutaneous Hydration Assessment in SCD

  • UPMC Sickle Cell Clinic, Pittsburgh
Mengambil peserta
Umur 12 ke atas · Semua jantina · Dikemas kini 12 Nov 2025 · NCT05210114

Recruitment and Engagement in Care to Impact Practice Enhancement (RECIPE) for Sickle Cell Disease

  • University of Pennsylvania, Philadelphia
Mengambil pesertaKajian pemerhatian
Umur 18 ke atas · Semua jantina · Dikemas kini 22 Jun 2025 · NCT06385886

Daripada ClinicalTrials.gov, data diperoleh pada 5 Okt 2026. Setiap kajian menetapkan kriteria kelayakannya sendiri; pasukan kajian menentukan siapa yang layak menyertai.