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Kajian klinikal Atrofi Otot Spinal di Florida

8 kajian untuk Atrofi Otot Spinal sedang mencari peserta di lokasi di Florida.

Bandar di Florida

Teks kajian rasmi (Bahasa Inggeris)

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy

  • University of Florida Pediatrics, Gainesville
Mengambil pesertaFasa 4
3 Months – 24 Months · Semua jantina · Dikemas kini 2 Okt 2026 · NCT05861986

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy

  • University of Florida Pediatrics, Gainesville
Mengambil pesertaFasa 4
3 Months – 24 Months · Semua jantina · Dikemas kini 10 Sep 2026 · NCT05861999

A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)

  • Nemours Children's Hospital, Orlando, Orlando
Mengambil pesertaFasa 1
Umur 3 ke atas · Semua jantina · Dikemas kini 3 Sep 2026 · NCT06555419

Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy

  • Nemours Children's Hospital, Florida, Orlando
Mengambil peserta
Umur 3 ke atas · Semua jantina · Dikemas kini 19 Ogo 2026 · NCT05866419

Clinical Procedures to Support Research in ALS

  • University of Miami, Miami
Mengambil pesertaKajian pemerhatian
Umur 18 ke atas · Semua jantina · Dikemas kini 15 Jun 2026 · NCT03489278

ALS/MND Natural History Study Data Repository

  • University of Florida, Gainesville
Mengambil pesertaKajian pemerhatian
Umur 18 hingga 90 · Semua jantina · Dikemas kini 20 Mei 2026 · NCT05966038

Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)

  • Golisano Children's Hospital of Southwest Florida, Fort Myers
  • Jackson South Medical Center, Palmetto Bay
Mengambil pesertaKajian pemerhatian
Semua umur · Semua jantina · Dikemas kini 31 Jan 2025 · NCT04174157

Daripada ClinicalTrials.gov, data diperoleh pada 5 Okt 2026. Setiap kajian menetapkan kriteria kelayakannya sendiri; pasukan kajian menentukan siapa yang layak menyertai.