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Kajian klinikal Atrofi Otot Spinal di Philadelphia, PA

7 kajian untuk Atrofi Otot Spinal sedang mencari peserta di lokasi dalam dan sekitar Philadelphia (dalam lingkungan kira-kira 30 batu). Buka kajian untuk melihat siapa yang layak menyertai dan cara menghubungi pasukan kajian.

Teks kajian rasmi (Bahasa Inggeris)

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A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy

Mengambil pesertaFasa 2
  • The Children's Hospital of Philadelphia, Philadelphia
Sehingga umur 2 · Semua jantina · Dikemas kini 2 Okt 2026 · NCT07047144

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy

Mengambil pesertaFasa 4
  • Children'S Hospital of Philadelphia, Philadelphia
3 Months – 24 Months · Semua jantina · Dikemas kini 2 Okt 2026 · NCT05861986

A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy

Mengambil pesertaFasa 2
  • Children's Hospital Philadelphia - Neurology, Philadelphia
Umur 5 hingga 17 · Semua jantina · Dikemas kini 14 Sep 2026 · NCT07287982

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy

Mengambil pesertaFasa 4
  • Children'S Hospital of Philadelphia, Philadelphia
3 Months – 24 Months · Semua jantina · Dikemas kini 10 Sep 2026 · NCT05861999

A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)

Mengambil pesertaFasa 1
  • Children's Hospital of Philadelphia, Philadelphia
Umur 3 ke atas · Semua jantina · Dikemas kini 3 Sep 2026 · NCT06555419

Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy

Mengambil peserta
  • Children's Hospital Philadelphia, Philadelphia
Umur 3 ke atas · Semua jantina · Dikemas kini 19 Ogo 2026 · NCT05866419

ALS/MND Natural History Study Data Repository

Mengambil pesertaKajian pemerhatian
  • Thomas Jefferson University, Philadelphia
  • Temple University Lewis Katz School of Medicine, Philadelphia
Umur 18 hingga 90 · Semua jantina · Dikemas kini 20 Mei 2026 · NCT05966038

Kajian Atrofi Otot Spinal di bandar lain

Kajian lain di Philadelphia

Daripada ClinicalTrials.gov, data diperoleh pada 6 Okt 2026. Setiap kajian menetapkan kriteria kelayakannya sendiri; pasukan kajian menentukan siapa yang layak menyertai.