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Utama › Atrofi Otot Spinal › New York › New York City

Kajian klinikal Atrofi Otot Spinal di New York City, NY

9 kajian untuk Atrofi Otot Spinal sedang mencari peserta di lokasi dalam dan sekitar New York City (dalam lingkungan kira-kira 30 batu). Buka kajian untuk melihat siapa yang layak menyertai dan cara menghubungi pasukan kajian.

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A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy

Mengambil pesertaFasa 4
  • Columbia University Medical Center, New York
3 Months – 24 Months · Semua jantina · Dikemas kini 2 Okt 2026 · NCT05861986

ASsessing The REAl-world Safety & Effectiveness of Spinal Muscular Atrophy Participants Treated With Intrathecal Onasemnogene Abeparvovec-brve (OAV101B) (ITVISMA®): A U.S. Pragmatic Multicenter Study (STREAM)

Mengambil pesertaFasa 4
  • Columbia University Medical Center, New York
Umur 2 hingga 100 · Semua jantina · Dikemas kini 18 Sep 2026 · NCT07448610

A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy

Mengambil pesertaFasa 2
  • Columbia University Herbert Irving Comprehensive Cancer Center, New York
Umur 5 hingga 17 · Semua jantina · Dikemas kini 14 Sep 2026 · NCT07287982

Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy

Mengambil peserta
  • Columbia University Irving Medical Center/NewYork Presbyterian Hospital, New York
Umur 3 ke atas · Semua jantina · Dikemas kini 19 Ogo 2026 · NCT05866419

Characterizing Perceived Physical Fatigability in Nusinersen-treated SMA

Mengambil pesertaKajian pemerhatian
  • Columbia University Irving Medical Center, New York
Umur 12 ke atas · Semua jantina · Dikemas kini 14 Mei 2026 · NCT06955897

Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders

Mengambil pesertaKajian pemerhatianSukarelawan sihat dialu-alukan
  • Columbia University Irving Medical Center, New York
Umur 5 ke atas · Semua jantina · Dikemas kini 9 Apr 2026 · NCT06839469

HABIT-ILE + FST in Children With SMA: Preliminary Effectiveness

Mengambil peserta
  • Center for Cerebral Palsy Research, Teachers College, Columbia University, New York
Umur 5 hingga 17 · Semua jantina · Dikemas kini 23 Mac 2026 · NCT07488338

Gait and Bone Health in SMA

Mengambil pesertaKajian pemerhatian
  • Columbia University Irving Medical Center, New York
Umur 8 hingga 50 · Semua jantina · Dikemas kini 18 Mac 2026 · NCT07400198

A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their Babies

Mengambil pesertaKajian pemerhatian
  • Columbia University Irving Medical Center, New York
Umur 18 hingga 54 · Wanita · Dikemas kini 9 Mac 2026 · NCT05789758

Kajian Atrofi Otot Spinal di bandar lain

Kajian lain di New York City

Daripada ClinicalTrials.gov, data diperoleh pada 6 Okt 2026. Setiap kajian menetapkan kriteria kelayakannya sendiri; pasukan kajian menentukan siapa yang layak menyertai.