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Gara Jalqabaatti › Dhukkuboota Dhalootaa › California

Qorannoo klinikaalii Dhukkuboota Dhalootaa California keessatti

Qorannoo 16 Dhukkuboota Dhalootaa f California keessatti hirmaatuu jiru.

Magaalota California keessatti

Takkalaa qorannoo (Ingiliffa)

Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network

  • University of California, Los Angeles, Los Angeles
  • University of California, Irvine Medical Center, Orange
  • Stanford University, Stanford
  • fi 2 dabalataa
Namoota walitti qabaa jiraQorannoo ilaalaaHojjettoota fayyaa simatamoo
1 Month – 100 Years · Saalaa hunda · Haaromfame 02-Onk-2026 · NCT02450851

Study to Evaluate the Efficacy and Safety of BMN 333 Versus Vosoritide in Children With Achondroplasia

  • UCSF Benioff Children's Hospital Oakland, Oakland
Namoota walitti qabaa jiraSadarkaa 2/3
Umuriin 2 hanga 17 · Saalaa hunda · Haaromfame 24-Ful-2026 · NCT07441876

A Long-Term Observational Study of Patients With Fucosidosis

  • Children's Hospital of Orange County, Orange
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 17-Ful-2026 · NCT07615400

Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study

  • UCLA Ataxia Center, Los Angeles
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Umuriin hundi · Saalaa hunda · Haaromfame 01-Ful-2026 · NCT06016946

Safety of Anumigilimab (CSL324) in Adults With Sickle Cell Disease (SCD)

  • University of California Irvine, Orange
Namoota walitti qabaa jiraSadarkaa 2
Umuriin 18 fi ol · Saalaa hunda · Haaromfame 05-Hag-2026 · NCT07224360

Prospective Clinical Assessment Study in Children With Hypochondroplasia

  • UCSF Benioff Children's Hospital, Oakland
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30 Months – 16 Years · Saalaa hunda · Haaromfame 16-Ado-2026 · NCT06410976

Rett Syndrome Registry

  • Children's Hospital Los Angeles, Los Angeles
  • UCSF Benioff Children's Hospital, Oakland
  • Rady Children's Hospital - San Diego, San Diego
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin 0 hanga 99 · Saalaa hunda · Haaromfame 30-Wax-2026 · NCT05432349

A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study

  • Ronald Reagan UCLA Medical Center, Los Angeles
  • University of Stanford Medical Center, Palo Alto
Namoota walitti qabaa jiraSadarkaa 1/2
Umuriin 1 fi ol · Saalaa hunda · Haaromfame 23-Bit-2026 · NCT05130437

Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia

  • UCSD Altman Clinical and Transalational Research Institute Building, Los Angeles
  • Ronald Reagan UCLA Medical Center, Los Angeles
  • Lucile Packard Children's Hospital Stanford, Stanford
Namoota walitti qabaa jiraSadarkaa 1/2
Umuriin hundi · Saalaa hunda · Haaromfame 22-Ama-2026 · NCT04159103

An Extension Study to Evaluate the Long-Term Safety and Clinical Activity of mRNA-3705 in Participants Previously Enrolled in Other Clinical Studies of mRNA-3705

  • UCLA Medical Center, Los Angeles
  • Lucile Packard Children's Hospital at Stanford, Palo Alto
  • Altman Clinical and Translational Research Institution, San Diego
Namoota walitti qabaa jiraSadarkaa 1/2
Umuriin 1 fi ol · Saalaa hunda · Haaromfame 23-Mud-2025 · NCT05295433

STXBP1 and SYNGAP1 Related Disorders Natural History Study

  • Stanford Medicine Children's Health, Palo Alto
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Umuriin hundi · Saalaa hunda · Haaromfame 29-Onk-2025 · NCT06555965

Large Language Models To Improve the Quality of Care of Cardiology Patients

  • Stanford, Palo Alto
Namoota walitti qabaa jira
Umuriin 18 fi ol · Saalaa hunda · Haaromfame 15-Cam-2025 · NCT06935253

Natural History Study of Patients with HPDL Mutations

  • Eun Hae Lee, San Diego
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 30-Bit-2025 · NCT05848271

An Adaptive Clinical Trial of BeginNGS Newborn Screening for Hundreds of Genetic Diseases by Genome Sequencing

  • Rady Children's Hospital San Diego, San Diego
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1 Day – 28 Days · Saalaa hunda · Haaromfame 12-Bit-2024 · NCT06306521

Rady Children's Institute Genomic Biorepository

  • Rady Pediatric Genomics & Systems Medicine Institute, San Diego
Namoota walitti qabaa jiraHojjettoota fayyaa simatamoo
Umuriin hundi · Saalaa hunda · Haaromfame 12-Mud-2022 · NCT02917460

Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.