Gara Jalqabaatti › Dhukkuboota Dhalootaa › Florida
Qorannoo klinikaalii Dhukkuboota Dhalootaa Florida keessatti
Qorannoo 7 Dhukkuboota Dhalootaa f Florida keessatti hirmaatuu jiru.
Magaalota Florida keessatti
Takkalaa qorannoo (Ingiliffa)
Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network
- University of Miami Miller School of Medicine, Miami
Namoota walitti qabaa jiraQorannoo ilaalaaHojjettoota fayyaa simatamoo
1 Month – 100 Years · Saalaa hunda · Haaromfame 02-Onk-2026 · NCT02450851Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study
- University of Florida - Neurology, Gainesville
- USF Ataxia Research Center, Tampa
Namoota walitti qabaa jiraQorannoo ilaalaaHojjettoota fayyaa simatamoo
Umuriin hundi · Saalaa hunda · Haaromfame 01-Ful-2026 · NCT06016946A Non-inferiority Pharmacokinetic and Safety/Tolerability Study of Two Different Doses of Weekly SC Alpha1-PI 15% Compared With Corresponding Standard IV Alpha1-PI in Participants With Alpha1-Antitrypsin Deficiency (AATD)
- GC2501 Study Site 103, Gainesville
- GC2501 Study Site 105, Miami
Namoota walitti qabaa jiraSadarkaa 3
Umuriin 18 hanga 80 · Saalaa hunda · Haaromfame 11-Hag-2026 · NCT07555483Safety of Anumigilimab (CSL324) in Adults With Sickle Cell Disease (SCD)
- The Foundation for Sickle Cell Disease, Hollywood
Namoota walitti qabaa jiraSadarkaa 2
Umuriin 18 fi ol · Saalaa hunda · Haaromfame 05-Hag-2026 · NCT07224360Rett Syndrome Registry
- Nicklaus Children's Hospital, Miami
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin 0 hanga 99 · Saalaa hunda · Haaromfame 30-Wax-2026 · NCT05432349A Study Investigating the Effectiveness and Safety of Garadacimab for Treating Patients With Hereditary Angioedema (HAE)
- Sirven and Associates, Miami
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin 12 fi ol · Saalaa hunda · Haaromfame 03-Wax-2026 · NCT07001280Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia
- Nicklaus Children's Hospital, Miami
- University of South Florida - 12901 Bruce B Downs, Tampa
Namoota walitti qabaa jiraSadarkaa 1/2
Umuriin hundi · Saalaa hunda · Haaromfame 22-Ama-2026 · NCT04159103Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.