🔎 Trials Near Me

Gara Jalqabaatti › Dhukkubaa Kuusaa Glycogen Gosa II › Pennsylvania

Qorannoo klinikaalii Dhukkubaa Kuusaa Glycogen Gosa II Pennsylvania keessatti

Qorannoo 4 Dhukkubaa Kuusaa Glycogen Gosa II f Pennsylvania keessatti hirmaatuu jiru.

Magaalota Pennsylvania keessatti

Takkalaa qorannoo (Ingiliffa)

A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)

  • Hospital of the University of Pennsylvania, Philadelphia
  • University of Pittsburgh Medical Center (UPMC), Pittsburgh
Namoota walitti qabaa jiraSadarkaa 1/2
Umuriin 18 hanga 65 · Saalaa hunda · Haaromfame 20-Ado-2026 · NCT07282847

Pompe Disease Registry Protocol

  • Penn State Health Milton South Hershey Medical Center- Site Number : 840126, Hershey
  • Children's Hospital of Philadelphia HUP Medical Genetics- Site Number : 840089, Philadelphia
  • Children's Hospital of Philadelphia- Site Number : 840034, Philadelphia
  • fi 2 dabalataa
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 23-Wax-2026 · NCT00231400

Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

  • University of Pennsylvania, Philadelphia
  • University of Pittsburgh School of Medicine, Pittsburgh
Namoota walitti qabaa jiraSadarkaa 2
Umuriin 18 fi ol · Saalaa hunda · Haaromfame 23-Wax-2026 · NCT07123155

A Global Prospective Observational Registry of Patients With Pompe Disease

  • University of Pennsylvania Perelman Center for Advanced Medicine, Philadelphia
  • University of Pittsburgh, Pittsburgh
  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 10-Bit-2026 · NCT06121011

Kanneen ClinicalTrials.gov irraa argaman, daataa 05-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.