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Gara Jalqabaatti › Dhukkubaa Kuusaa Glycogen Gosa II › Pennsylvania › Philadelphia

Qorannoo klinikaalii Dhukkubaa Kuusaa Glycogen Gosa II Philadelphia, PA keessatti

Qorannoo 4 Dhukkubaa Kuusaa Glycogen Gosa II f Philadelphia fi naannoo isaa (kilomeetira 30 keessatti) hirmaatuu jiru. Qorannoo banaa eenyu akka hirmaatu fi akkamitti garee qorannoo akka quunnaman ilaali.

Takkalaa qorannoo (Ingiliffa)

Qorannoo hirmaatuu barbaadduu? Fuula kana jalatti agarsiisi — $99 guyyaa 30f →

A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)

Namoota walitti qabaa jiraSadarkaa 1/2
  • Hospital of the University of Pennsylvania, Philadelphia
Umuriin 18 hanga 65 · Saalaa hunda · Haaromfame 20-Ado-2026 · NCT07282847

Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

Namoota walitti qabaa jiraSadarkaa 2
  • University of Pennsylvania, Philadelphia
Umuriin 18 fi ol · Saalaa hunda · Haaromfame 23-Wax-2026 · NCT07123155

Pompe Disease Registry Protocol

Namoota walitti qabaa jiraQorannoo ilaalaa
  • Children's Hospital of Philadelphia HUP Medical Genetics- Site Number : 840089, Philadelphia
  • Children's Hospital of Philadelphia- Site Number : 840034, Philadelphia
Umuriin hundi · Saalaa hunda · Haaromfame 23-Wax-2026 · NCT00231400

A Global Prospective Observational Registry of Patients With Pompe Disease

Namoota walitti qabaa jiraQorannoo ilaalaa
  • University of Pennsylvania Perelman Center for Advanced Medicine, Philadelphia
Umuriin hundi · Saalaa hunda · Haaromfame 10-Bit-2026 · NCT06121011

Qorannoo Dhukkubaa Kuusaa Glycogen Gosa II magaalota biroo keessatti

Qorannoo biroo Philadelphia keessatti

Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.