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Long-term Follow-up (LTFU) Study of Participants in Any iECURE Protocol Using an Investigational Product (IP)

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7 Months – 15 Months · Saalaa hunda · Haaromfame 31-Hag-2026 · NCT06805695

Study of LNP.UCD.ABE in Patients With Urea Cycle Disorders

Namoota walitti qabaa jiraSadarkaa 1/2
24 Hours – 5 Years · Saalaa hunda · Haaromfame 26-Hag-2026 · NCT07667387

Functional Evaluation in Patients With Urea Cycle Disorders (UCD) During a Driving Task

Namoota walitti qabaa jiraQorannoo ilaalaaHojjettoota fayyaa simatamoo
Umuriin 16 hanga 40 · Saalaa hunda · Haaromfame 31-Ado-2026 · NCT07701694

At Home Ammonia Monitoring of Inborn Errors of Ammonia Metabolism

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Umuriin 12 fi ol · Saalaa hunda · Haaromfame 27-Cam-2026 · NCT06953505

Hepatic Histopathology in Urea Cycle Disorders

Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 20-Ado-2025 · NCT04908319

Systemic Biomarkers of Brain Injury From Hyperammonemia

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Umuriin 7 hanga 18 · Saalaa hunda · Haaromfame 07-Gur-2024 · NCT04602325

Orphan Europe Carbaglu® Surveillance Protocol

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Umuriin hundi · Saalaa hunda · Haaromfame 07-Gur-2024 · NCT03409003

Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.