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Gara Jalqabaatti › Leukoencephalopathies › California

Qorannoo klinikaalii Leukoencephalopathies California keessatti

Qorannoo 4 Leukoencephalopathies f California keessatti hirmaatuu jiru.

Magaalota California keessatti

Takkalaa qorannoo (Ingiliffa)

A Study of AAV9 Gene Therapy in Participants With Canavan Disease (CANaspire Clinical Trial)

  • UCSF Benioff Children's Hospital Oakland, Oakland
Namoota walitti qabaa jiraSadarkaa 1/2
30 Months · Saalaa hunda · Haaromfame 17-Elb-2026 · NCT04998396

North American Mitochondrial Disease Consortium Patient Registry and Biorepository (NAMDC)

  • University of California San Diego, San Diego
  • Lucile Packard Children's Hospital, Stanford
Namoota walitti qabaa jiraQorannoo ilaalaaHojjettoota fayyaa simatamoo
Umuriin hundi · Saalaa hunda · Haaromfame 04-Gur-2026 · NCT01694940

The Myelin Disorders Biorepository Project

  • Children's Hospital of Los Angeles, Los Angeles
  • Children's Hospital of Orange County, Orange
  • Stanford University (Lucile Packard Children's Hospital), Palo Alto
  • fi 3 dabalataa
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 23-Onk-2025 · NCT03047369

Natural History Study of Patients with HPDL Mutations

  • Eun Hae Lee, San Diego
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 30-Bit-2025 · NCT05848271

Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.