Gara Jalqabaatti › Leukoencephalopathies › California
Qorannoo klinikaalii Leukoencephalopathies California keessatti
Qorannoo 4 Leukoencephalopathies f California keessatti hirmaatuu jiru.
Magaalota California keessatti
Takkalaa qorannoo (Ingiliffa)
A Study of AAV9 Gene Therapy in Participants With Canavan Disease (CANaspire Clinical Trial)
- UCSF Benioff Children's Hospital Oakland, Oakland
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30 Months · Saalaa hunda · Haaromfame 17-Elb-2026 · NCT04998396North American Mitochondrial Disease Consortium Patient Registry and Biorepository (NAMDC)
- University of California San Diego, San Diego
- Lucile Packard Children's Hospital, Stanford
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Umuriin hundi · Saalaa hunda · Haaromfame 04-Gur-2026 · NCT01694940The Myelin Disorders Biorepository Project
- Children's Hospital of Los Angeles, Los Angeles
- Children's Hospital of Orange County, Orange
- Stanford University (Lucile Packard Children's Hospital), Palo Alto
- fi 3 dabalataa
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Umuriin hundi · Saalaa hunda · Haaromfame 23-Onk-2025 · NCT03047369Natural History Study of Patients with HPDL Mutations
- Eun Hae Lee, San Diego
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Umuriin hundi · Saalaa hunda · Haaromfame 30-Bit-2025 · NCT05848271Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.