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Gara Jalqabaatti › Leukoencephalopathies

Qorannoo klinikaalii Leukoencephalopathies Ameerikaa Keessatti hirmaatuu

Qorannoo 7 Leukoencephalopathies f bakka adda addaa Ameerikaa Keessatti hirmaatuu jiru.

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An Open-Label Exploratory Study of Fosigotifator in Participants With Vanishing White Matter Disease

Namoota walitti qabaa jiraSadarkaa 1/2
6 Months · Saalaa hunda · Haaromfame 24-Ful-2026 · NCT05757141

A Study of AAV9 Gene Therapy in Participants With Canavan Disease (CANaspire Clinical Trial)

Namoota walitti qabaa jiraSadarkaa 1/2
30 Months · Saalaa hunda · Haaromfame 17-Elb-2026 · NCT04998396

Longitudinal Study of Neurodegenerative Disorders

Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 09-Gur-2026 · NCT03333200

North American Mitochondrial Disease Consortium Patient Registry and Biorepository (NAMDC)

Namoota walitti qabaa jiraQorannoo ilaalaaHojjettoota fayyaa simatamoo
Umuriin hundi · Saalaa hunda · Haaromfame 04-Gur-2026 · NCT01694940

The Myelin Disorders Biorepository Project

Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 23-Onk-2025 · NCT03047369

Natural History Study of Patients with HPDL Mutations

Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 30-Bit-2025 · NCT05848271

Natural History Study of Leukoencephalopathy With Brainstem and Spinal Cord Involvement and Lactate Elevation (LBSL)

Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 03-Ado-2024 · NCT03624374

Kanneen ClinicalTrials.gov irraa argaman, daataa 05-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.