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Gara Jalqabaatti › Leukoencephalopathies › Pennsylvania

Qorannoo klinikaalii Leukoencephalopathies Pennsylvania keessatti

Qorannoo 4 Leukoencephalopathies f Pennsylvania keessatti hirmaatuu jiru.

Magaalota Pennsylvania keessatti

Takkalaa qorannoo (Ingiliffa)

An Open-Label Exploratory Study of Fosigotifator in Participants With Vanishing White Matter Disease

  • Children's Hospital of Philadelphia, Philadelphia
Namoota walitti qabaa jiraSadarkaa 1/2
6 Months · Saalaa hunda · Haaromfame 24-Ful-2026 · NCT05757141

Longitudinal Study of Neurodegenerative Disorders

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 09-Gur-2026 · NCT03333200

North American Mitochondrial Disease Consortium Patient Registry and Biorepository (NAMDC)

  • The Children's Hospital of Philadelphia, Philadelphia
  • Children's Hospital of Pittsburgh, Pittsburgh
Namoota walitti qabaa jiraQorannoo ilaalaaHojjettoota fayyaa simatamoo
Umuriin hundi · Saalaa hunda · Haaromfame 04-Gur-2026 · NCT01694940

The Myelin Disorders Biorepository Project

  • The Children's Hospital of Philadelphia, Philadelphia
  • University of Pennsylvania, Philadelphia
  • University of Pittsburgh Medical Center, Pittsburgh
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 23-Onk-2025 · NCT03047369

Kanneen ClinicalTrials.gov irraa argaman, daataa 05-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.