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Qorannoo klinikaalii Dhibbee Uumamaa California keessatti

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Takkalaa qorannoo (Ingiliffa)

Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network

  • University of California, Los Angeles, Los Angeles
  • University of California, Irvine Medical Center, Orange
  • Stanford University, Stanford
  • fi 2 dabalataa
Namoota walitti qabaa jiraQorannoo ilaalaaHojjettoota fayyaa simatamoo
1 Month – 100 Years · Saalaa hunda · Haaromfame 02-Onk-2026 · NCT02450851

A Study of SGT-212 Gene Therapy in Friedreich's Ataxia

  • The University of California, Los Angeles (UCLA), Los Angeles
Namoota walitti qabaa jiraSadarkaa 1
Umuriin 18 hanga 40 · Saalaa hunda · Haaromfame 29-Ful-2026 · NCT07180355

A First-in-human Study of KK8123 in Adults With X-linked Hypophosphatemia

  • University of California - San Francisco, San Francisco
Namoota walitti qabaa jiraSadarkaa 1/2
Umuriin 18 hanga 65 · Saalaa hunda · Haaromfame 21-Ful-2026 · NCT06525636

Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study

  • UCLA Ataxia Center, Los Angeles
Namoota walitti qabaa jiraQorannoo ilaalaaHojjettoota fayyaa simatamoo
Umuriin hundi · Saalaa hunda · Haaromfame 01-Ful-2026 · NCT06016946

International Rare Brain Tumor Registry

  • Children's Hospital Los Angeles, Los Angeles
  • University of California San Francisco, San Francisco
Namoota walitti qabaa jiraQorannoo ilaalaa
Hanga umuriin 45 · Saalaa hunda · Haaromfame 07-Hag-2026 · NCT05697874

Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

  • University of California - Irvine Medical Center, Irvine
Namoota walitti qabaa jiraSadarkaa 2
Umuriin 18 fi ol · Saalaa hunda · Haaromfame 23-Wax-2026 · NCT07123155

A Study of AAV9 Gene Therapy in Participants With Canavan Disease (CANaspire Clinical Trial)

  • UCSF Benioff Children's Hospital Oakland, Oakland
Namoota walitti qabaa jiraSadarkaa 1/2
30 Months · Saalaa hunda · Haaromfame 17-Elb-2026 · NCT04998396

The ExTINGUISH Trial of Inebilizumab in NMDAR Encephalitis

  • Children's Hospital of Orange County, Orange
  • UC Irvine, Orange
  • UC Davis, Sacramento
Namoota walitti qabaa jiraSadarkaa 2
Umuriin 12 fi ol · Saalaa hunda · Haaromfame 01-Ado-2025 · NCT04372615

Prospective Observational International Registry of Patients With Newly Diagnosed Peripheral T Cell Lymphoma.

  • Stanford University, Stanford
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin 18 fi ol · Saalaa hunda · Haaromfame 06-Cam-2025 · NCT03964480

Epilepsy Learning Healthcare System (ELHS)

  • Children's Hospital Los Angeles, Los Angeles
  • University of Southern California, Los Angeles
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 30-Hag-2024 · NCT06265103

Kanneen ClinicalTrials.gov irraa argaman, daataa 05-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.