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Takkalaa qorannoo (Ingiliffa)
Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network
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1 Month – 100 Years · Saalaa hunda · Haaromfame 02-Onk-2026 · NCT02450851Genetic Study to Determine the Cause of Birth Defects in Newborns in Texas
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1 Day – 90 Days · Saalaa hunda · Haaromfame 01-Onk-2026 · NCT07102966Odevixibat Pregnancy and Lactation Surveillance Program: A Study to Evaluate the Safety of Odevixibat During Pregnancy and/or Lactation
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Umuriin hundi · Dubartoota · Haaromfame 01-Onk-2026 · NCT06258902A Study of SGT-212 Gene Therapy in Friedreich's Ataxia
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Umuriin 18 hanga 40 · Saalaa hunda · Haaromfame 29-Ful-2026 · NCT07180355RAPA-501 Therapy for ALS
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Umuriin 18 fi ol · Saalaa hunda · Haaromfame 29-Ful-2026 · NCT04220190Diagnosis and Treatment of Patients With Inborn Errors of Metabolism
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1 Month – 115 Years · Saalaa hunda · Haaromfame 22-Ful-2026 · NCT00369421Human Biospecimen Procurement Protocol: Biorepository to Support Translational Research to Identify Disease Mechanism(s)
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1 Month – 100 Years · Saalaa hunda · Haaromfame 22-Ful-2026 · NCT02543996A First-in-human Study of KK8123 in Adults With X-linked Hypophosphatemia
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Umuriin 18 hanga 65 · Saalaa hunda · Haaromfame 21-Ful-2026 · NCT06525636Caregiving Networks Across Disease Context and the Life Course
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Umuriin 18 hanga 100 · Saalaa hunda · Haaromfame 15-Ful-2026 · NCT05007990Longitudinal Studies of Patient With FPDMM
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1 Day – 100 Years · Saalaa hunda · Haaromfame 11-Ful-2026 · NCT03854318Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study
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Umuriin hundi · Saalaa hunda · Haaromfame 01-Ful-2026 · NCT06016946Elafibranor Pregnancy Surveillance Program: A Study to Evaluate the Safety of Elafibranor During Pregnancy
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Umuriin hundi · Dubartoota · Haaromfame 31-Hag-2026 · NCT07556913International Rare Brain Tumor Registry
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Hanga umuriin 45 · Saalaa hunda · Haaromfame 07-Hag-2026 · NCT05697874Stakeholders of Rare Diseases Informing Values In Neuroethics
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Umuriin hundi · Saalaa hunda · Haaromfame 13-Ado-2026 · NCT07314736Evaluation of an Advanced Lower Extremity Neuroprostheses
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Umuriin 21 hanga 75 · Saalaa hunda · Haaromfame 10-Ado-2026 · NCT00623389A Study Evaluating the Real-World Experience of Givinostat in Patients With Duchenne Muscular Dystrophy
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Umuriin 6 fi ol · Saalaa hunda · Haaromfame 02-Ado-2026 · NCT07127978Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)
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Umuriin 18 fi ol · Saalaa hunda · Haaromfame 23-Wax-2026 · NCT07123155Baker Gordon Syndrome Natural History Study
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Umuriin 0 hanga 99 · Saalaa hunda · Haaromfame 03-Wax-2026 · NCT06399952UW Undiagnosed Genetic Diseases Program
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Hanga umuriin 100 · Saalaa hunda · Haaromfame 29-Cam-2026 · NCT04586075Direct to Patient Minimal Risk Biospecimen and Data Collection Research
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Umuriin 18 hanga 90 · Saalaa hunda · Haaromfame 05-Cam-2026 · NCT07128966A Randomized Study of SPK-10001 Gene Therapy in Participants With Huntington's Disease
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Umuriin 25 hanga 65 · Saalaa hunda · Haaromfame 05-Cam-2026 · NCT06826612A Study of AAV9 Gene Therapy in Participants With Canavan Disease (CANaspire Clinical Trial)
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30 Months · Saalaa hunda · Haaromfame 17-Elb-2026 · NCT04998396Gene Discovery Core, The Manton Center
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Umuriin hundi · Saalaa hunda · Haaromfame 25-Bit-2026 · NCT02743845Delineating the Molecular Spectrum and the Clinical, Imaging and Neuronal Phenotype of Chopra-Amiel-Gordon Syndrome
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Umuriin hundi · Saalaa hunda · Haaromfame 17-Gur-2026 · NCT05528744MIHRA - Patient-Rooted Insights for Shaping Myositis Science (PRISMS)
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Umuriin 7 fi ol · Saalaa hunda · Haaromfame 28-Ama-2026 · NCT07374107Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.