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Qorannoo klinikaalii Dhibbee Uumamaa Pennsylvania keessatti

Qorannoo 7 Dhibbee Uumamaa f Pennsylvania keessatti hirmaatuu jiru.

Magaalota Pennsylvania keessatti

Takkalaa qorannoo (Ingiliffa)

Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network

  • University of Pennsylvania, Philadelphia
  • Children's Hospital of Philadelphia, Philadelphia
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1 Month – 100 Years · Saalaa hunda · Haaromfame 02-Onk-2026 · NCT02450851

A Study of SGT-212 Gene Therapy in Friedreich's Ataxia

  • The Children's Hospital of Philadelphia (CHOP), Philadelphia
Namoota walitti qabaa jiraSadarkaa 1
Umuriin 18 hanga 40 · Saalaa hunda · Haaromfame 29-Ful-2026 · NCT07180355

Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study

  • Children's Hospital of Philadelphia, Philadelphia
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Umuriin hundi · Saalaa hunda · Haaromfame 01-Ful-2026 · NCT06016946

Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

  • University of Pennsylvania, Philadelphia
  • University of Pittsburgh School of Medicine, Pittsburgh
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Umuriin 18 fi ol · Saalaa hunda · Haaromfame 23-Wax-2026 · NCT07123155

A Randomized Study of SPK-10001 Gene Therapy in Participants With Huntington's Disease

  • University of Pennsylvania, Philadelphia
  • University of Pittsburg, Pittsburgh
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Umuriin 25 hanga 65 · Saalaa hunda · Haaromfame 05-Cam-2026 · NCT06826612

The ExTINGUISH Trial of Inebilizumab in NMDAR Encephalitis

  • University of Pennsylvania, Philadelphia
  • University of Pittsburgh, Pittsburgh
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Umuriin 12 fi ol · Saalaa hunda · Haaromfame 01-Ado-2025 · NCT04372615

Epilepsy Learning Healthcare System (ELHS)

  • Penn State Hershey, Hershey
  • Children's Hospital of Philadelphia (CHOP), Philadelphia
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Umuriin hundi · Saalaa hunda · Haaromfame 30-Hag-2024 · NCT06265103

Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.