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Qorannoo klinikaalii Atrophy Muscular Sirna Caddii Florida keessatti

Qorannoo 8 Atrophy Muscular Sirna Caddii f Florida keessatti hirmaatuu jiru.

Magaalota Florida keessatti

Takkalaa qorannoo (Ingiliffa)

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy

  • University of Florida Pediatrics, Gainesville
Namoota walitti qabaa jiraSadarkaa 4
3 Months – 24 Months · Saalaa hunda · Haaromfame 02-Onk-2026 · NCT05861986

A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy

  • Rare Disease Research FL LLC, Kissimmee
Namoota walitti qabaa jiraSadarkaa 2
Umuriin 5 hanga 17 · Saalaa hunda · Haaromfame 14-Ful-2026 · NCT07287982

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy

  • University of Florida Pediatrics, Gainesville
Namoota walitti qabaa jiraSadarkaa 4
3 Months – 24 Months · Saalaa hunda · Haaromfame 10-Ful-2026 · NCT05861999

A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)

  • Nemours Children's Hospital, Orlando, Orlando
Namoota walitti qabaa jiraSadarkaa 1
Umuriin 3 fi ol · Saalaa hunda · Haaromfame 03-Ful-2026 · NCT06555419

Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy

  • Nemours Children's Hospital, Florida, Orlando
Namoota walitti qabaa jira
Umuriin 3 fi ol · Saalaa hunda · Haaromfame 19-Hag-2026 · NCT05866419

Clinical Procedures to Support Research in ALS

  • University of Miami, Miami
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin 18 fi ol · Saalaa hunda · Haaromfame 15-Wax-2026 · NCT03489278

ALS/MND Natural History Study Data Repository

  • University of Florida, Gainesville
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin 18 hanga 90 · Saalaa hunda · Haaromfame 20-Cam-2026 · NCT05966038

Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)

  • Golisano Children's Hospital of Southwest Florida, Fort Myers
  • Jackson South Medical Center, Palmetto Bay
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 31-Ama-2025 · NCT04174157

Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.