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Qorannoo klinikaalii Atrophy Muscular Sirna Caddii Massachusetts keessatti

Qorannoo 6 Atrophy Muscular Sirna Caddii f Massachusetts keessatti hirmaatuu jiru.

Magaalota Massachusetts keessatti

Takkalaa qorannoo (Ingiliffa)

A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy

  • Boston Children's Hospital, Boston
Namoota walitti qabaa jiraSadarkaa 2
Umuriin 5 hanga 17 · Saalaa hunda · Haaromfame 14-Ful-2026 · NCT07287982

A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)

  • Boston Children's Hospital, Boston
Namoota walitti qabaa jiraSadarkaa 1
Umuriin 3 fi ol · Saalaa hunda · Haaromfame 03-Ful-2026 · NCT06555419

Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy

  • Boston Children's Hospital, Boston
Namoota walitti qabaa jira
Umuriin 3 fi ol · Saalaa hunda · Haaromfame 19-Hag-2026 · NCT05866419

ALS/MND Natural History Study Data Repository

  • Lahey Clinic, Burlington
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin 18 hanga 90 · Saalaa hunda · Haaromfame 20-Cam-2026 · NCT05966038

Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders

  • Boston Children's Hospital, Boston
Namoota walitti qabaa jiraQorannoo ilaalaaHojjettoota fayyaa simatamoo
Umuriin 5 fi ol · Saalaa hunda · Haaromfame 09-Elb-2026 · NCT06839469

A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their Babies

  • Boston Children's Hospital, Boston
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin 18 hanga 54 · Dubartoota · Haaromfame 09-Bit-2026 · NCT05789758

Kanneen ClinicalTrials.gov irraa argaman, daataa 05-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.