Gara Jalqabaatti › Atrophy Muscular Sirna Caddii › Massachusetts
Qorannoo klinikaalii Atrophy Muscular Sirna Caddii Massachusetts keessatti
Qorannoo 6 Atrophy Muscular Sirna Caddii f Massachusetts keessatti hirmaatuu jiru.
Magaalota Massachusetts keessatti
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A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- Boston Children's Hospital, Boston
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Umuriin 5 hanga 17 · Saalaa hunda · Haaromfame 14-Ful-2026 · NCT07287982A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)
- Boston Children's Hospital, Boston
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Umuriin 3 fi ol · Saalaa hunda · Haaromfame 03-Ful-2026 · NCT06555419Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy
- Boston Children's Hospital, Boston
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Umuriin 3 fi ol · Saalaa hunda · Haaromfame 19-Hag-2026 · NCT05866419ALS/MND Natural History Study Data Repository
- Lahey Clinic, Burlington
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Umuriin 18 hanga 90 · Saalaa hunda · Haaromfame 20-Cam-2026 · NCT05966038Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders
- Boston Children's Hospital, Boston
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Umuriin 5 fi ol · Saalaa hunda · Haaromfame 09-Elb-2026 · NCT06839469A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their Babies
- Boston Children's Hospital, Boston
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Umuriin 18 hanga 54 · Dubartoota · Haaromfame 09-Bit-2026 · NCT05789758Kanneen ClinicalTrials.gov irraa argaman, daataa 05-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.