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Gara Jalqabaatti › Atrophy Muscular Sirna Caddii › Massachusetts › Boston

Qorannoo klinikaalii Atrophy Muscular Sirna Caddii Boston, MA keessatti

Qorannoo 5 Atrophy Muscular Sirna Caddii f Boston fi naannoo isaa (kilomeetira 30 keessatti) hirmaatuu jiru. Qorannoo banaa eenyu akka hirmaatu fi akkamitti garee qorannoo akka quunnaman ilaali.

Takkalaa qorannoo (Ingiliffa)

Qorannoo hirmaatuu barbaadduu? Fuula kana jalatti agarsiisi — $99 guyyaa 30f →

A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy

Namoota walitti qabaa jiraSadarkaa 2
  • Boston Children's Hospital, Boston
Umuriin 5 hanga 17 · Saalaa hunda · Haaromfame 14-Ful-2026 · NCT07287982

A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)

Namoota walitti qabaa jiraSadarkaa 1
  • Boston Children's Hospital, Boston
Umuriin 3 fi ol · Saalaa hunda · Haaromfame 03-Ful-2026 · NCT06555419

Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy

Namoota walitti qabaa jira
  • Boston Children's Hospital, Boston
Umuriin 3 fi ol · Saalaa hunda · Haaromfame 19-Hag-2026 · NCT05866419

Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders

Namoota walitti qabaa jiraQorannoo ilaalaaHojjettoota fayyaa simatamoo
  • Boston Children's Hospital, Boston
Umuriin 5 fi ol · Saalaa hunda · Haaromfame 09-Elb-2026 · NCT06839469

A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their Babies

Namoota walitti qabaa jiraQorannoo ilaalaa
  • Boston Children's Hospital, Boston
Umuriin 18 hanga 54 · Dubartoota · Haaromfame 09-Bit-2026 · NCT05789758

Qorannoo Atrophy Muscular Sirna Caddii magaalota biroo keessatti

Qorannoo biroo Boston keessatti

Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.