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Qorannoo klinikaalii Atrophy Muscular Sirna Caddii North Carolina keessatti

Qorannoo 3 Atrophy Muscular Sirna Caddii f North Carolina keessatti hirmaatuu jiru.

Magaalota North Carolina keessatti

Takkalaa qorannoo (Ingiliffa)

A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy

  • Rare Disease Research NC, LLC, Hillsborough
Namoota walitti qabaa jiraSadarkaa 2
Umuriin 5 hanga 17 · Saalaa hunda · Haaromfame 14-Ful-2026 · NCT07287982

Clinical Procedures to Support Research in ALS

  • Duke University, Durham
  • Wake Forest University, Winston-Salem
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin 18 fi ol · Saalaa hunda · Haaromfame 15-Wax-2026 · NCT03489278

Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)

  • Duke Health, Durham
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 31-Ama-2025 · NCT04174157

Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.