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Gara Jalqabaatti › Atrophy Muscular Sirna Caddii › Pennsylvania › Philadelphia

Qorannoo klinikaalii Atrophy Muscular Sirna Caddii Philadelphia, PA keessatti

Qorannoo 7 Atrophy Muscular Sirna Caddii f Philadelphia fi naannoo isaa (kilomeetira 30 keessatti) hirmaatuu jiru. Qorannoo banaa eenyu akka hirmaatu fi akkamitti garee qorannoo akka quunnaman ilaali.

Takkalaa qorannoo (Ingiliffa)

Qorannoo hirmaatuu barbaadduu? Fuula kana jalatti agarsiisi — $99 guyyaa 30f →

A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy

Namoota walitti qabaa jiraSadarkaa 2
  • The Children's Hospital of Philadelphia, Philadelphia
Hanga umuriin 2 · Saalaa hunda · Haaromfame 02-Onk-2026 · NCT07047144

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy

Namoota walitti qabaa jiraSadarkaa 4
  • Children'S Hospital of Philadelphia, Philadelphia
3 Months – 24 Months · Saalaa hunda · Haaromfame 02-Onk-2026 · NCT05861986

A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy

Namoota walitti qabaa jiraSadarkaa 2
  • Children's Hospital Philadelphia - Neurology, Philadelphia
Umuriin 5 hanga 17 · Saalaa hunda · Haaromfame 14-Ful-2026 · NCT07287982

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy

Namoota walitti qabaa jiraSadarkaa 4
  • Children'S Hospital of Philadelphia, Philadelphia
3 Months – 24 Months · Saalaa hunda · Haaromfame 10-Ful-2026 · NCT05861999

A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)

Namoota walitti qabaa jiraSadarkaa 1
  • Children's Hospital of Philadelphia, Philadelphia
Umuriin 3 fi ol · Saalaa hunda · Haaromfame 03-Ful-2026 · NCT06555419

Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy

Namoota walitti qabaa jira
  • Children's Hospital Philadelphia, Philadelphia
Umuriin 3 fi ol · Saalaa hunda · Haaromfame 19-Hag-2026 · NCT05866419

ALS/MND Natural History Study Data Repository

Namoota walitti qabaa jiraQorannoo ilaalaa
  • Thomas Jefferson University, Philadelphia
  • Temple University Lewis Katz School of Medicine, Philadelphia
Umuriin 18 hanga 90 · Saalaa hunda · Haaromfame 20-Cam-2026 · NCT05966038

Qorannoo Atrophy Muscular Sirna Caddii magaalota biroo keessatti

Qorannoo biroo Philadelphia keessatti

Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.