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Ensaios clínicos de Doença Falciforme em Pensilvânia

20 estudos para Doença Falciforme estão buscando participantes em locais em Pensilvânia.

Cidades em Pensilvânia

Texto oficial do estudo (Inglês)

A Study to Investigate the Efficacy and Safety of Crizanlizumab (5 mg/kg) Compared With Placebo in Adolescent and Adult Sickle Cell Disease Patients Who Experience Frequent Vaso-Occlusive Crises (SPARKLE)

  • Spoknwrdclinicaltrials, Easton
  • Thomas Jefferson University Me, Philadelphia
RecrutandoFase 3
Idades de 12 a 100 · Todos os sexos · Atualizado em 28 de set. de 2026 · NCT06439082

A Phase 1b, Open-Label Study of DISC-3405 in Participants With Sickle Cell Disease (SCD)

  • University of Pittsburgh Medical Center (UPMC), Pittsburgh
RecrutandoFase 1
Idades 18 e acima · Todos os sexos · Atualizado em 23 de set. de 2026 · NCT07187973

A Study to Evaluate How Well Etavopivat Works in People With Sickle Cell Disease

  • Children's Hosptl Philadelphia, Philadelphia
  • St Christopher Hosp for Child, Philadelphia
RecrutandoFase 3
Idades 12 e acima · Todos os sexos · Atualizado em 17 de set. de 2026 · NCT06612268

A Phase I/II Study of ITU512 in Healthy Participants and Patients With Sickle Cell Disease

  • Childrens Hospital Of Philadelphia, Philadelphia
RecrutandoFase 1/2Voluntários saudáveis bem-vindos
Idades de 12 a 55 · Todos os sexos · Atualizado em 9 de set. de 2026 · NCT06546670

A Study to Evaluate BMS-986470 in Healthy Volunteers and Participants With Sickle Cell Disease

  • Local Institution - 0029, Philadelphia
  • Thomas Jefferson University - Medicine/GI and Hepatology, Philadelphia
  • Local Institution - 0032, Pittsburgh
RecrutandoFase 1/2Voluntários saudáveis bem-vindos
Idades 18 e acima · Todos os sexos · Atualizado em 18 de ago. de 2026 · NCT06481306

ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders

  • Children's Hospital of Philadelphia, Philadelphia
  • Penn Comprehensive Hemophilia and Thrombophilia Program/Hospital of the University of Pennsylvania, Philadelphia
  • St. Christopher's Hospital for Children, Philadelphia
  • e mais 1
RecrutandoEstudo observacional
Todas as idades · Todos os sexos · Atualizado em 17 de ago. de 2026 · NCT04398628

Safety, Efficacy, and Pharmacokinetics of CSL889 in Adults and Adolescents With Sickle Cell Disease During Vaso-Occlusive Crisis

  • University of Pittsburgh, Pittsburgh
  • Hillman Cancer Center, Pittsburgh
RecrutandoFase 2
Idades 12 e acima · Todos os sexos · Atualizado em 14 de ago. de 2026 · NCT06699849

T-Cell Depleted Alternative Donor Bone Marrow Transplant for Sickle Cell Disease (SCD) and Other Anemias

  • Children's Hospital of Pittsburgh of UPMC, Pittsburgh
RecrutandoFase 1/2
Idades de 5 a 40 · Todos os sexos · Atualizado em 13 de ago. de 2026 · NCT03653338

Ruxolitinib-Enhanced Haplo HCT for Children and Young Adults With Sickle Cell Disease

  • Children's Hospital of Philadelphia, Philadelphia
RecrutandoFase 1/2
Idades de 12 a 45 · Todos os sexos · Atualizado em 4 de jun. de 2026 · NCT07252050

Comparing the Effectiveness of Matched Related Donor Hematopoietic Stem Cell Transplantation to Disease Modifying Therapy in Pediatric Patients With Sickle Cell Disease

  • Children's Hospital of Philadelphia (MRD-HCT), Philadelphia
RecrutandoEstudo observacional
Idades de 3 a 20 · Todos os sexos · Atualizado em 4 de jun. de 2026 · NCT06941389

Clinical and Biomarker Effects of Depot Medroxyprogesterone Acetate in Females With Sickle Cell Disease

  • Children's Hospital of Philadelphia, Philadelphia
RecrutandoFase 4
Idades de 18 a 50 · Mulheres · Atualizado em 28 de mai. de 2026 · NCT06665997

A Socio-ecological Approach for Improving Self-management in Adolescents With SCD

  • Children's Hospital of Philadelphia, Philadelphia
Recrutando
Idades de 13 a 21 · Todos os sexos · Atualizado em 11 de mai. de 2026 · NCT06290401

Zinc Supplementation in Sickle Cell Disease: A Precursor to the Think Zinc for Bones Trial

  • Children's Hospital of Philadelphia, Philadelphia
  • Thomas Jefferson University Hospital, Philadelphia
RecrutandoFase 2
Idades de 15 a 40 · Todos os sexos · Atualizado em 13 de mar. de 2026 · NCT06260891

Stress Management and Mindfulness Intervention for Patients With Sickle Cell Disease

  • University of Pennsylvania, Philadelphia
Recrutando
Idades 18 e acima · Todos os sexos · Atualizado em 27 de fev. de 2026 · NCT07316478

A Long-term Follow-up Study in Patients Who Received BEAM-101

  • Children's Hospital of Philadelphia, Philadelphia
RecrutandoEstudo observacional
Idades de 14 a 37 · Todos os sexos · Atualizado em 28 de jan. de 2026 · NCT07373639

Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
RecrutandoEstudo observacional
2 Months – 60 Years · Todos os sexos · Atualizado em 13 de jan. de 2026 · NCT04528355

Peer Support for Adolescents and Emerging Adults With Sickle Cell Pain

  • UPMC University of Pittsburgh Classical Hematology Adult Clinic, Pittsburgh
  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
Recrutando
Idades de 16 a 30 · Todos os sexos · Atualizado em 7 de jan. de 2026 · NCT06374238

Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
RecrutandoFase 2
2 Months – 55 Years · Todos os sexos · Atualizado em 15 de dez. de 2025 · NCT01962415

Cutaneous Hydration Assessment in SCD

  • UPMC Sickle Cell Clinic, Pittsburgh
Recrutando
Idades 12 e acima · Todos os sexos · Atualizado em 12 de nov. de 2025 · NCT05210114

Recruitment and Engagement in Care to Impact Practice Enhancement (RECIPE) for Sickle Cell Disease

  • University of Pennsylvania, Philadelphia
RecrutandoEstudo observacional
Idades 18 e acima · Todos os sexos · Atualizado em 22 de jun. de 2025 · NCT06385886

Fonte: ClinicalTrials.gov, dados obtidos em 5 de out. de 2026. Cada estudo define seus próprios critérios de elegibilidade; a equipe do estudo decide quem pode participar.