Hem › Spinal muskelatrofi › New York
Kliniska studier för Spinal muskelatrofi i New York
10 studier för Spinal muskelatrofi söker deltagare vid platser i New York.
Städer i New York
Officiell studietext (engelska)
A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
- Columbia University Medical Center, New York
RekryterarFas 4
3 Months – 24 Months · Alla kön · Uppdaterad 2 okt. 2026 · NCT05861986ASsessing The REAl-world Safety & Effectiveness of Spinal Muscular Atrophy Participants Treated With Intrathecal Onasemnogene Abeparvovec-brve (OAV101B) (ITVISMA®): A U.S. Pragmatic Multicenter Study (STREAM)
- Columbia University Medical Center, New York
RekryterarFas 4
Ålder 2 till 100 · Alla kön · Uppdaterad 18 sep. 2026 · NCT07448610A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- Columbia University Herbert Irving Comprehensive Cancer Center, New York
RekryterarFas 2
Ålder 5 till 17 · Alla kön · Uppdaterad 14 sep. 2026 · NCT07287982Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy
- Columbia University Irving Medical Center/NewYork Presbyterian Hospital, New York
Rekryterar
Ålder 3 och äldre · Alla kön · Uppdaterad 19 aug. 2026 · NCT05866419Characterizing Perceived Physical Fatigability in Nusinersen-treated SMA
- Columbia University Irving Medical Center, New York
RekryterarObservationsstudie
Ålder 12 och äldre · Alla kön · Uppdaterad 14 maj 2026 · NCT06955897Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders
- Columbia University Irving Medical Center, New York
RekryterarObservationsstudieFriska volontärer välkomna
Ålder 5 och äldre · Alla kön · Uppdaterad 9 apr. 2026 · NCT06839469HABIT-ILE + FST in Children With SMA: Preliminary Effectiveness
- Center for Cerebral Palsy Research, Teachers College, Columbia University, New York
Rekryterar
Ålder 5 till 17 · Alla kön · Uppdaterad 23 mars 2026 · NCT07488338Gait and Bone Health in SMA
- Columbia University Irving Medical Center, New York
RekryterarObservationsstudie
Ålder 8 till 50 · Alla kön · Uppdaterad 18 mars 2026 · NCT07400198A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their Babies
- Columbia University Irving Medical Center, New York
RekryterarObservationsstudie
Ålder 18 till 54 · Kvinnor · Uppdaterad 9 mars 2026 · NCT05789758Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)
- University of Rochester Medical Center, Rochester
- The State University of New York, Stony Brook
RekryterarObservationsstudie
Alla åldrar · Alla kön · Uppdaterad 31 jan. 2025 · NCT04174157Från ClinicalTrials.gov, data hämtad 5 okt. 2026. Varje studie har egna kvalifikationskrav; studieteamet avgör vem som kan delta.