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Kliniska studier för Spinal muskelatrofi i New York

10 studier för Spinal muskelatrofi söker deltagare vid platser i New York.

Städer i New York

Officiell studietext (engelska)

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy

  • Columbia University Medical Center, New York
RekryterarFas 4
3 Months – 24 Months · Alla kön · Uppdaterad 2 okt. 2026 · NCT05861986

A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy

  • Columbia University Herbert Irving Comprehensive Cancer Center, New York
RekryterarFas 2
Ålder 5 till 17 · Alla kön · Uppdaterad 14 sep. 2026 · NCT07287982

Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy

  • Columbia University Irving Medical Center/NewYork Presbyterian Hospital, New York
Rekryterar
Ålder 3 och äldre · Alla kön · Uppdaterad 19 aug. 2026 · NCT05866419

Characterizing Perceived Physical Fatigability in Nusinersen-treated SMA

  • Columbia University Irving Medical Center, New York
RekryterarObservationsstudie
Ålder 12 och äldre · Alla kön · Uppdaterad 14 maj 2026 · NCT06955897

Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders

  • Columbia University Irving Medical Center, New York
RekryterarObservationsstudieFriska volontärer välkomna
Ålder 5 och äldre · Alla kön · Uppdaterad 9 apr. 2026 · NCT06839469

HABIT-ILE + FST in Children With SMA: Preliminary Effectiveness

  • Center for Cerebral Palsy Research, Teachers College, Columbia University, New York
Rekryterar
Ålder 5 till 17 · Alla kön · Uppdaterad 23 mars 2026 · NCT07488338

Gait and Bone Health in SMA

  • Columbia University Irving Medical Center, New York
RekryterarObservationsstudie
Ålder 8 till 50 · Alla kön · Uppdaterad 18 mars 2026 · NCT07400198

A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their Babies

  • Columbia University Irving Medical Center, New York
RekryterarObservationsstudie
Ålder 18 till 54 · Kvinnor · Uppdaterad 9 mars 2026 · NCT05789758

Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)

  • University of Rochester Medical Center, Rochester
  • The State University of New York, Stony Brook
RekryterarObservationsstudie
Alla åldrar · Alla kön · Uppdaterad 31 jan. 2025 · NCT04174157

Från ClinicalTrials.gov, data hämtad 5 okt. 2026. Varje studie har egna kvalifikationskrav; studieteamet avgör vem som kan delta.