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Pag-aaral pangklinika para sa Spinal Muscular Atrophy sa New York

10 pag-aaral para sa Spinal Muscular Atrophy ang naghahanap ng mga kalahok sa mga site sa New York.

Mga Lungsod sa New York

Opisyal na teksto ng pag-aaral (English)

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy

  • Columbia University Medical Center, New York
Nagre-recruitPhase 4
3 Months – 24 Months · Lahat ng kasarian · Na-update Okt 2, 2026 · NCT05861986

ASsessing The REAl-world Safety & Effectiveness of Spinal Muscular Atrophy Participants Treated With Intrathecal Onasemnogene Abeparvovec-brve (OAV101B) (ITVISMA®): A U.S. Pragmatic Multicenter Study (STREAM)

  • Columbia University Medical Center, New York
Nagre-recruitPhase 4
Edad 2 hanggang 100 · Lahat ng kasarian · Na-update Set 18, 2026 · NCT07448610

A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy

  • Columbia University Herbert Irving Comprehensive Cancer Center, New York
Nagre-recruitPhase 2
Edad 5 hanggang 17 · Lahat ng kasarian · Na-update Set 14, 2026 · NCT07287982

Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy

  • Columbia University Irving Medical Center/NewYork Presbyterian Hospital, New York
Nagre-recruit
Edad 3 pataas · Lahat ng kasarian · Na-update Ago 19, 2026 · NCT05866419

Characterizing Perceived Physical Fatigability in Nusinersen-treated SMA

  • Columbia University Irving Medical Center, New York
Nagre-recruitObservasyonal na pag-aaral
Edad 12 pataas · Lahat ng kasarian · Na-update May 14, 2026 · NCT06955897

Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders

  • Columbia University Irving Medical Center, New York
Nagre-recruitObservasyonal na pag-aaralMalugod na tinatanggap ang malusog na boluntaryo
Edad 5 pataas · Lahat ng kasarian · Na-update Abr 9, 2026 · NCT06839469

HABIT-ILE + FST in Children With SMA: Preliminary Effectiveness

  • Center for Cerebral Palsy Research, Teachers College, Columbia University, New York
Nagre-recruit
Edad 5 hanggang 17 · Lahat ng kasarian · Na-update Mar 23, 2026 · NCT07488338

Gait and Bone Health in SMA

  • Columbia University Irving Medical Center, New York
Nagre-recruitObservasyonal na pag-aaral
Edad 8 hanggang 50 · Lahat ng kasarian · Na-update Mar 18, 2026 · NCT07400198

A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their Babies

  • Columbia University Irving Medical Center, New York
Nagre-recruitObservasyonal na pag-aaral
Edad 18 hanggang 54 · Kababaihan · Na-update Mar 9, 2026 · NCT05789758

Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)

  • University of Rochester Medical Center, Rochester
  • The State University of New York, Stony Brook
Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update Ene 31, 2025 · NCT04174157

Mula sa ClinicalTrials.gov, na-kuha noong Okt 6, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.