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Etid klinik pou Maladi Depo Glikojèn Tip II nan Pennsylvania
4 etid pou Maladi Depo Glikojèn Tip II ap chèche patisipan nan sit nan Pennsylvania.
Vil nan Pennsylvania
Tèks ofisyèl etid la (Anglè)
A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)
- Hospital of the University of Pennsylvania, Philadelphia
- University of Pittsburgh Medical Center (UPMC), Pittsburgh
Ap rekriteFaz 1/2
Laj 18 a 65 · Tout sèks · Mizajou Jul 20, 2026 · NCT07282847Pompe Disease Registry Protocol
- Penn State Health Milton South Hershey Medical Center- Site Number : 840126, Hershey
- Children's Hospital of Philadelphia HUP Medical Genetics- Site Number : 840089, Philadelphia
- Children's Hospital of Philadelphia- Site Number : 840034, Philadelphia
- ak 2 plis
Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Jun 23, 2026 · NCT00231400Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)
- University of Pennsylvania, Philadelphia
- University of Pittsburgh School of Medicine, Pittsburgh
Ap rekriteFaz 2
Laj 18 ak plis · Tout sèks · Mizajou Jun 23, 2026 · NCT07123155A Global Prospective Observational Registry of Patients With Pompe Disease
- University of Pennsylvania Perelman Center for Advanced Medicine, Philadelphia
- University of Pittsburgh, Pittsburgh
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Mar 10, 2026 · NCT06121011Sous ClinicalTrials.gov, done yo ranmase Oct 5, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.