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Akèy › Maladi Depo Glikojèn Tip II › Pennsylvania › Pittsburgh

Etid klinik pou Maladi Depo Glikojèn Tip II nan Pittsburgh, PA

4 etid pou Maladi Depo Glikojèn Tip II ap chèche patisipan nan sit nan ak bò kote Pittsburgh (nan yon distans apeprè 30 mil). Louvri yon etid pou wè ki moun ki ka patisipe ak kijan pou kontakte ekip etid la.

Tèks ofisyèl etid la (Anglè)

Ap chèche patisipan pou yon etid? Mete l anwo paj sa a — $99 pou 30 jou →

A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)

Ap rekriteFaz 1/2
  • University of Pittsburgh Medical Center (UPMC), Pittsburgh
Laj 18 a 65 · Tout sèks · Mizajou Jul 20, 2026 · NCT07282847

Pompe Disease Registry Protocol

Ap rekriteEtid obsèvasyon
  • UPMC Children's Hospital of Pittsburgh- Site Number : 840014, Pittsburgh
  • UPMC Children's Hospital of Pittsburgh- Site Number : 840023, Pittsburgh
Tout laj · Tout sèks · Mizajou Jun 23, 2026 · NCT00231400

Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

Ap rekriteFaz 2
  • University of Pittsburgh School of Medicine, Pittsburgh
Laj 18 ak plis · Tout sèks · Mizajou Jun 23, 2026 · NCT07123155

A Global Prospective Observational Registry of Patients With Pompe Disease

Ap rekriteEtid obsèvasyon
  • University of Pittsburgh, Pittsburgh
  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
Tout laj · Tout sèks · Mizajou Mar 10, 2026 · NCT06121011

Etid Maladi Depo Glikojèn Tip II nan lòt vil

Lòt etid nan Pittsburgh

Sous ClinicalTrials.gov, done yo ranmase Oct 5, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.