Akèy › Maladi Depo Glikojèn Tip II › Pennsylvania › Philadelphia
Etid klinik pou Maladi Depo Glikojèn Tip II nan Philadelphia, PA
4 etid pou Maladi Depo Glikojèn Tip II ap chèche patisipan nan sit nan ak bò kote Philadelphia (nan yon distans apeprè 30 mil). Louvri yon etid pou wè ki moun ki ka patisipe ak kijan pou kontakte ekip etid la.
Tèks ofisyèl etid la (Anglè)
Ap chèche patisipan pou yon etid? Mete l anwo paj sa a — $99 pou 30 jou →
A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)
Ap rekriteFaz 1/2
- Hospital of the University of Pennsylvania, Philadelphia
Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)
Ap rekriteFaz 2
- University of Pennsylvania, Philadelphia
Pompe Disease Registry Protocol
Ap rekriteEtid obsèvasyon
- Children's Hospital of Philadelphia HUP Medical Genetics- Site Number : 840089, Philadelphia
- Children's Hospital of Philadelphia- Site Number : 840034, Philadelphia
A Global Prospective Observational Registry of Patients With Pompe Disease
Ap rekriteEtid obsèvasyon
- University of Pennsylvania Perelman Center for Advanced Medicine, Philadelphia
Etid Maladi Depo Glikojèn Tip II nan lòt vil
- Durham, NC8 etid
- Irvine, CA5 etid
- St. Louis, MO5 etid
- Arlington, VA5 etid
- Pittsburgh, PA4 etid
- Atlanta, GA4 etid
- New York City, NY4 etid
- Indianapolis, IN3 etid
- Jacksonville, FL3 etid
- Cincinnati, OH3 etid
- Phoenix, AZ3 etid
Lòt etid nan Philadelphia
- Kansè (tout kalite)59 etid
- Kansè nan tete56 etid
- Kansè Poumon ki pa ti selil51 etid
- Kansè Metastatik46 etid
- Kansè pwostat44 etid
- Kansè kolorektal44 etid
- Kansè ovè44 etid
- Kansè poumon36 etid
- Leksemi mieloïd egi34 etid
- Ensifizyans kadyak31 etid
- Kansè Endomèt28 etid
- Depresyon26 etid
Sous ClinicalTrials.gov, done yo ranmase Oct 6, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.