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Akèy › Maladi Depo Glikojèn Tip II › Pennsylvania › Philadelphia

Etid klinik pou Maladi Depo Glikojèn Tip II nan Philadelphia, PA

4 etid pou Maladi Depo Glikojèn Tip II ap chèche patisipan nan sit nan ak bò kote Philadelphia (nan yon distans apeprè 30 mil). Louvri yon etid pou wè ki moun ki ka patisipe ak kijan pou kontakte ekip etid la.

Tèks ofisyèl etid la (Anglè)

Ap chèche patisipan pou yon etid? Mete l anwo paj sa a — $99 pou 30 jou →

A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)

Ap rekriteFaz 1/2
  • Hospital of the University of Pennsylvania, Philadelphia
Laj 18 a 65 · Tout sèks · Mizajou Jul 20, 2026 · NCT07282847

Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

Ap rekriteFaz 2
  • University of Pennsylvania, Philadelphia
Laj 18 ak plis · Tout sèks · Mizajou Jun 23, 2026 · NCT07123155

Pompe Disease Registry Protocol

Ap rekriteEtid obsèvasyon
  • Children's Hospital of Philadelphia HUP Medical Genetics- Site Number : 840089, Philadelphia
  • Children's Hospital of Philadelphia- Site Number : 840034, Philadelphia
Tout laj · Tout sèks · Mizajou Jun 23, 2026 · NCT00231400

A Global Prospective Observational Registry of Patients With Pompe Disease

Ap rekriteEtid obsèvasyon
  • University of Pennsylvania Perelman Center for Advanced Medicine, Philadelphia
Tout laj · Tout sèks · Mizajou Mar 10, 2026 · NCT06121011

Etid Maladi Depo Glikojèn Tip II nan lòt vil

Lòt etid nan Philadelphia

Sous ClinicalTrials.gov, done yo ranmase Oct 6, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.