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Kliniske studier for Spinal muskelatrofi i New York
10 studier for Spinal muskelatrofi søker deltakere på steder i New York.
Byer i New York
Offisiell studietekst (engelsk)
A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
- Columbia University Medical Center, New York
RekruttererFase 4
3 Months – 24 Months · Alle kjønn · Oppdatert 2. okt. 2026 · NCT05861986ASsessing The REAl-world Safety & Effectiveness of Spinal Muscular Atrophy Participants Treated With Intrathecal Onasemnogene Abeparvovec-brve (OAV101B) (ITVISMA®): A U.S. Pragmatic Multicenter Study (STREAM)
- Columbia University Medical Center, New York
RekruttererFase 4
Alder 2 til 100 · Alle kjønn · Oppdatert 18. sep. 2026 · NCT07448610A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- Columbia University Herbert Irving Comprehensive Cancer Center, New York
RekruttererFase 2
Alder 5 til 17 · Alle kjønn · Oppdatert 14. sep. 2026 · NCT07287982Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy
- Columbia University Irving Medical Center/NewYork Presbyterian Hospital, New York
Rekrutterer
Alder 3 og eldre · Alle kjønn · Oppdatert 19. aug. 2026 · NCT05866419Characterizing Perceived Physical Fatigability in Nusinersen-treated SMA
- Columbia University Irving Medical Center, New York
RekruttererObservasjonsstudie
Alder 12 og eldre · Alle kjønn · Oppdatert 14. mai 2026 · NCT06955897Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders
- Columbia University Irving Medical Center, New York
RekruttererObservasjonsstudieFrivillige helsepersonell ønskes velkommen
Alder 5 og eldre · Alle kjønn · Oppdatert 9. apr. 2026 · NCT06839469HABIT-ILE + FST in Children With SMA: Preliminary Effectiveness
- Center for Cerebral Palsy Research, Teachers College, Columbia University, New York
Rekrutterer
Alder 5 til 17 · Alle kjønn · Oppdatert 23. mar. 2026 · NCT07488338Gait and Bone Health in SMA
- Columbia University Irving Medical Center, New York
RekruttererObservasjonsstudie
Alder 8 til 50 · Alle kjønn · Oppdatert 18. mar. 2026 · NCT07400198A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their Babies
- Columbia University Irving Medical Center, New York
RekruttererObservasjonsstudie
Alder 18 til 54 · Kvinner · Oppdatert 9. mar. 2026 · NCT05789758Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)
- University of Rochester Medical Center, Rochester
- The State University of New York, Stony Brook
RekruttererObservasjonsstudie
Alle aldre · Alle kjønn · Oppdatert 31. jan. 2025 · NCT04174157Fra ClinicalTrials.gov, data hentet 5. okt. 2026. Hver studie setter sine egne kvalifikasjonskrav; studieteamet avgjør hvem som kan delta.