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Kliniske studier for Spinal muskelatrofi i New York City, NY
9 studier for Spinal muskelatrofi søker deltakere på steder i og rundt New York City (innen ca. 30 miles). Åpne et studie for å se hvem som kan delta og hvordan du kontakter studieteamet.
Offisiell studietekst (engelsk)
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A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
RekruttererFase 4
- Columbia University Medical Center, New York
ASsessing The REAl-world Safety & Effectiveness of Spinal Muscular Atrophy Participants Treated With Intrathecal Onasemnogene Abeparvovec-brve (OAV101B) (ITVISMA®): A U.S. Pragmatic Multicenter Study (STREAM)
RekruttererFase 4
- Columbia University Medical Center, New York
A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
RekruttererFase 2
- Columbia University Herbert Irving Comprehensive Cancer Center, New York
Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy
Rekrutterer
- Columbia University Irving Medical Center/NewYork Presbyterian Hospital, New York
Characterizing Perceived Physical Fatigability in Nusinersen-treated SMA
RekruttererObservasjonsstudie
- Columbia University Irving Medical Center, New York
Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders
RekruttererObservasjonsstudieFrivillige helsepersonell ønskes velkommen
- Columbia University Irving Medical Center, New York
HABIT-ILE + FST in Children With SMA: Preliminary Effectiveness
Rekrutterer
- Center for Cerebral Palsy Research, Teachers College, Columbia University, New York
Gait and Bone Health in SMA
RekruttererObservasjonsstudie
- Columbia University Irving Medical Center, New York
A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their Babies
RekruttererObservasjonsstudie
- Columbia University Irving Medical Center, New York
Spinal muskelatrofi-studier i andre byer
- Mountain View, CA9 studier
- Philadelphia, PA7 studier
- Grand Rapids, MI6 studier
- Chicago, IL6 studier
- Norfolk, VA6 studier
- Houston, TX5 studier
- Boston, MA5 studier
- Phoenix, AZ4 studier
- Lewisville, TX4 studier
- Little Rock, AR4 studier
- Aurora, CO4 studier
- Memphis, TN3 studier
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Fra ClinicalTrials.gov, data hentet 6. okt. 2026. Hver studie setter sine egne kvalifikasjonskrav; studieteamet avgjør hvem som kan delta.