Gara Jalqabaatti › Atrophy Muscular Sirna Caddii › New York
Qorannoo klinikaalii Atrophy Muscular Sirna Caddii New York keessatti
Qorannoo 10 Atrophy Muscular Sirna Caddii f New York keessatti hirmaatuu jiru.
Magaalota New York keessatti
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A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
- Columbia University Medical Center, New York
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3 Months – 24 Months · Saalaa hunda · Haaromfame 02-Onk-2026 · NCT05861986ASsessing The REAl-world Safety & Effectiveness of Spinal Muscular Atrophy Participants Treated With Intrathecal Onasemnogene Abeparvovec-brve (OAV101B) (ITVISMA®): A U.S. Pragmatic Multicenter Study (STREAM)
- Columbia University Medical Center, New York
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Umuriin 2 hanga 100 · Saalaa hunda · Haaromfame 18-Ful-2026 · NCT07448610A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- Columbia University Herbert Irving Comprehensive Cancer Center, New York
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Umuriin 5 hanga 17 · Saalaa hunda · Haaromfame 14-Ful-2026 · NCT07287982Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy
- Columbia University Irving Medical Center/NewYork Presbyterian Hospital, New York
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Umuriin 3 fi ol · Saalaa hunda · Haaromfame 19-Hag-2026 · NCT05866419Characterizing Perceived Physical Fatigability in Nusinersen-treated SMA
- Columbia University Irving Medical Center, New York
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Umuriin 12 fi ol · Saalaa hunda · Haaromfame 14-Cam-2026 · NCT06955897Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders
- Columbia University Irving Medical Center, New York
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Umuriin 5 fi ol · Saalaa hunda · Haaromfame 09-Elb-2026 · NCT06839469HABIT-ILE + FST in Children With SMA: Preliminary Effectiveness
- Center for Cerebral Palsy Research, Teachers College, Columbia University, New York
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Umuriin 5 hanga 17 · Saalaa hunda · Haaromfame 23-Bit-2026 · NCT07488338Gait and Bone Health in SMA
- Columbia University Irving Medical Center, New York
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Umuriin 8 hanga 50 · Saalaa hunda · Haaromfame 18-Bit-2026 · NCT07400198A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their Babies
- Columbia University Irving Medical Center, New York
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Umuriin 18 hanga 54 · Dubartoota · Haaromfame 09-Bit-2026 · NCT05789758Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)
- University of Rochester Medical Center, Rochester
- The State University of New York, Stony Brook
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Umuriin hundi · Saalaa hunda · Haaromfame 31-Ama-2025 · NCT04174157Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.