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Spinal Muscular Atrophy clinical trials in Philadelphia, PA
7 studies for Spinal Muscular Atrophy are looking for participants at sites in and around Philadelphia (within about 30 miles). Open a study to see who can join and how to contact the study team.
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A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy
RecruitingPhase 2
- The Children's Hospital of Philadelphia, Philadelphia
A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
RecruitingPhase 4
- Children'S Hospital of Philadelphia, Philadelphia
A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
RecruitingPhase 2
- Children's Hospital Philadelphia - Neurology, Philadelphia
A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy
RecruitingPhase 4
- Children'S Hospital of Philadelphia, Philadelphia
A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)
RecruitingPhase 1
- Children's Hospital of Philadelphia, Philadelphia
Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy
Recruiting
- Children's Hospital Philadelphia, Philadelphia
ALS/MND Natural History Study Data Repository
RecruitingObservational study
- Thomas Jefferson University, Philadelphia
- Temple University Lewis Katz School of Medicine, Philadelphia
About Spinal Muscular Atrophy
Spinal muscular atrophy (SMA) attacks nerve cells in the spinal cord, weakening voluntary muscles. Read about the genetics, types, and what may help.
More about Spinal Muscular Atrophy on MedlinePlus
Spinal Muscular Atrophy trials in other cities
- New York City, NY9 studies
- Mountain View, CA9 studies
- Grand Rapids, MI6 studies
- Norfolk, VA6 studies
- Chicago, IL6 studies
- Houston, TX5 studies
- Boston, MA5 studies
- Phoenix, AZ4 studies
- Lewisville, TX4 studies
- Little Rock, AR4 studies
- Aurora, CO4 studies
- Memphis, TN3 studies
Other studies in Philadelphia
- Cancer (all types)59 studies
- Breast Cancer56 studies
- Non-Small Cell Lung Cancer51 studies
- Metastatic Cancer46 studies
- Prostate Cancer44 studies
- Colorectal Cancer44 studies
- Ovarian Cancer44 studies
- Lung Cancer36 studies
- Acute Myeloid Leukemia34 studies
- Heart Failure31 studies
- Endometrial Cancer28 studies
- Depression26 studies
From ClinicalTrials.gov, data retrieved Oct 6, 2026. Each study sets its own eligibility; the study team decides who can join.